Orphan Drugs Market: Global Industry Trends, Share, Size, Growth, Opportunity and Forecast 2023-2028

Orphan Drugs Market: Global Industry Trends, Share, Size, Growth, Opportunity and Forecast 2023-2028


The global orphan drugs market size reached US$ 191.7 Billion in 2022. Looking forward, IMARC Group expects the market to reach US$ 383.5 Billion by 2028, exhibiting a growth rate (CAGR) of 12.02% during 2023-2028.

Orphan drugs refer to pharmaceutical products used for the diagnosis, prevention and treatment of rare medical disorders. These drugs are manufactured to meet a specific public health requirement and usually have a limited market as they are produced for a small group of patients. They are effective against numerous oncological, metabolic, hematologic, immunologic, infectious and neurological diseases. Medical ailments, such as lymphoma, leukemia, cystic fibrosis, glioma, pancreatic cancer, ovarian cancer, multiple myeloma and renal cell carcinoma, are often life-threatening, chronic, progressive, degenerative and disabling and require specific treatment alternatives that are effective for their particular symptoms.

Orphan Drugs Market Trends:
The increasing prevalence of cancer and other rare genetic disorders is one of the key factors driving the growth of the market. Pharmaceutical manufacturers are developing innovative orphan drugs to provide personalized therapy to patients. The market is also being driven by increasing awareness among the masses regarding the benefits of orphan drugs. The emergence of new pharmaceutical drug manufacturers and the implementation of favorable government policies to inhibit the spread of contagious diseases are also contributing to the market growth. Additionally, various product innovations, such as the development of biological orphan drugs, are acting as other growth-inducing factors. These drugs can treat diseases, such as cancer, and reverse the damage caused to the stem cells, which is facilitating their overall demand significantly. Other factors, including improvements in the healthcare infrastructure, along with extensive research and development (R&D) activities, are expected to drive the market further.

Key Market Segmentation:
IMARC Group provides an analysis of the key trends in each sub-segment of the global orphan drugs market report, along with forecasts at the global, regional and country level from 2023-2028. Our report has categorized the market based on drug type, disease type, phase, top selling drugs and distribution channel.

Breakup by Drug Type:

Biological
Non-Biological

Breakup by Disease Type:

Oncology
Hematology
Neurology
Cardiovascular
Others

Breakup by Phase:

Phase I
Phase II
Phase III
Phase IV

Breakup by Top Selling Drugs:

Revlimid
Rituxan
Copaxone
Opdivo
Keytruda
Imbruvica
Avonex
Sensipar
Soliris
Others

Breakup by Distribution Channel:

Hospital Pharmacies
Retail Pharmacies
Online Stores
Others

Breakup by Region:

North America
United States
Canada
Asia Pacific
China
Japan
India
South Korea
Australia
Indonesia
Others
Europe
Germany
France
United Kingdom
Italy
Spain
Russia
Others
Latin America
Brazil
Mexico
Others
Middle East and Africa

Competitive Landscape:
The report has also analysed the competitive landscape of the market with some of the key players being AbbVie Inc., Alexion Pharmaceuticals Inc., Amgen Inc., Biogen Inc., Bristol-Myers Squibb Company, F. Hoffmann-La Roche AG (Roche Holding AG), Jazz Pharmaceuticals Plc, Johnson & Johnson, Merck & Co. Inc., Novartis AG, Pfizer Inc., Sanofi S.A., Takeda Pharmaceutical Company Limited and Teva Pharmaceutical Industries Ltd.

Key Questions Answered in This Report

1. What was the size of the global orphan drugs market in 2022?
2. What is the expected growth rate of the global orphan drugs market during 2023-2028?
3. What are the key factors driving the global orphan drugs market?
4. What has been the impact of COVID-19 on the global orphan drugs market?
5. What is the breakup of the global orphan drugs market based on the drug type?
6. What is the breakup of the global orphan drugs market based on the disease type?
7. What is the breakup of the global orphan drugs market based on top selling drugs?
8. What is the breakup of the global orphan drugs market based on the distribution channel?
9. What are the key regions in the global orphan drugs market?
10. Who are the key players/companies in the global orphan drugs market?


1 Preface
2 Scope and Methodology 
2.1 Objectives of the Study
2.2 Stakeholders
2.3 Data Sources
2.3.1 Primary Sources
2.3.2 Secondary Sources
2.4 Market Estimation
2.4.1 Bottom-Up Approach
2.4.2 Top-Down Approach
2.5 Forecasting Methodology
3 Executive Summary
4 Introduction
4.1 Overview
4.2 Key Industry Trends
5 Global Orphan Drugs Market
5.1 Market Overview
5.2 Market Performance
5.3 Impact of COVID-19
5.4 Market Forecast
6 Market Breakup by Drug Type
6.1 Biological
6.1.1 Market Trends
6.1.2 Market Forecast
6.2 Non-Biological
6.2.1 Market Trends
6.2.2 Market Forecast
7 Market Breakup by Disease Type
7.1 Oncology
7.1.1 Market Trends
7.1.2 Market Forecast
7.2 Hematology
7.2.1 Market Trends
7.2.2 Market Forecast
7.3 Neurology
7.3.1 Market Trends
7.3.2 Market Forecast
7.4 Cardiovascular
7.4.1 Market Trends
7.4.2 Market Forecast
7.5 Others
7.5.1 Market Trends
7.5.2 Market Forecast
8 Market Breakup by Phase
8.1 Phase I
8.1.1 Market Trends
8.1.2 Market Forecast
8.2 Phase II
8.2.1 Market Trends
8.2.2 Market Forecast
8.3 Phase III
8.3.1 Market Trends
8.3.2 Market Forecast
8.4 Phase IV
8.4.1 Market Trends
8.4.2 Market Forecast
9 Market Breakup by Top Selling Drugs
9.1 Revlimid
9.1.1 Market Trends
9.1.2 Market Forecast
9.2 Rituxan
9.2.1 Market Trends
9.2.2 Market Forecast
9.3 Copaxone
9.3.1 Market Trends
9.3.2 Market Forecast
9.4 Opdivo
9.4.1 Market Trends
9.4.2 Market Forecast
9.5 Keytruda
9.5.1 Market Trends
9.5.2 Market Forecast
9.6 Imbruvica
9.6.1 Market Trends
9.6.2 Market Forecast
9.7 Avonex
9.7.1 Market Trends
9.7.2 Market Forecast
9.8 Sensipar
9.8.1 Market Trends
9.8.2 Market Forecast
9.9 Soliris
9.9.1 Market Trends
9.9.2 Market Forecast
9.10 Others
9.10.1 Market Trends
9.10.2 Market Forecast
10  Market Breakup by Distribution Channel
10.1 Hospital Pharmacies
10.1.1 Market Trends
10.1.2 Market Forecast
10.2 Retail Pharmacies
10.2.1 Market Trends
10.2.2 Market Forecast
10.3 Online Stores
10.3.1 Market Trends
10.3.2 Market Forecast
10.4 Others
10.4.1 Market Trends
10.4.2 Market Forecast
11  Market Breakup by Region
11.1 North America
11.1.1 United States
 11.1.1.1 Market Trends
 11.1.1.2 Market Forecast
11.1.2 Canada
 11.1.2.1 Market Trends
 11.1.2.2 Market Forecast
11.2 Asia Pacific
11.2.1 China
 11.2.1.1 Market Trends
 11.2.1.2 Market Forecast
11.2.2 Japan
 11.2.2.1 Market Trends
 11.2.2.2 Market Forecast
11.2.3 India
 11.2.3.1 Market Trends
 11.2.3.2 Market Forecast
11.2.4 South Korea
 11.2.4.1 Market Trends
 11.2.4.2 Market Forecast
11.2.5 Australia
 11.2.5.1 Market Trends
 11.2.5.2 Market Forecast
11.2.6 Indonesia
 11.2.6.1 Market Trends
 11.2.6.2 Market Forecast
11.2.7 Others
 11.2.7.1 Market Trends
 11.2.7.2 Market Forecast
11.3 Europe
11.3.1 Germany
 11.3.1.1 Market Trends
 11.3.1.2 Market Forecast
11.3.2 France
 11.3.2.1 Market Trends
 11.3.2.2 Market Forecast
11.3.3 United Kingdom
 11.3.3.1 Market Trends
 11.3.3.2 Market Forecast
11.3.4 Italy
 11.3.4.1 Market Trends
 11.3.4.2 Market Forecast
11.3.5 Spain
 11.3.5.1 Market Trends
 11.3.5.2 Market Forecast
11.3.6 Russia
 11.3.6.1 Market Trends
 11.3.6.2 Market Forecast
11.3.7 Others
 11.3.7.1 Market Trends
 11.3.7.2 Market Forecast
11.4 Latin America
11.4.1 Brazil
 11.4.1.1 Market Trends
 11.4.1.2 Market Forecast
11.4.2 Mexico
 11.4.2.1 Market Trends
 11.4.2.2 Market Forecast
11.4.3 Others
 11.4.3.1 Market Trends
 11.4.3.2 Market Forecast
11.5 Middle East and Africa
11.5.1 Market Trends
11.5.2 Market Breakup by Country
11.5.3 Market Forecast
12  SWOT Analysis
12.1 Overview
12.2 Strengths
12.3 Weaknesses
12.4 Opportunities
12.5 Threats
13  Value Chain Analysis
14  Porters Five Forces Analysis
14.1 Overview
14.2 Bargaining Power of Buyers
14.3 Bargaining Power of Suppliers
14.4 Degree of Competition
14.5 Threat of New Entrants
14.6 Threat of Substitutes
15  Price Analysis
16  Competitive Landscape
16.1 Market Structure
16.2 Key Players
16.3 Profiles of Key Players
16.3.1 AbbVie Inc.
 16.3.1.1 Company Overview
 16.3.1.2 Product Portfolio 
 16.3.1.3 Financials
 16.3.1.4 SWOT Analysis
16.3.2 Alexion Pharmaceuticals Inc.
 16.3.2.1 Company Overview
 16.3.2.2 Product Portfolio 
 16.3.2.3 Financials
 16.3.2.4 SWOT Analysis
16.3.3 Amgen Inc.
 16.3.3.1 Company Overview
 16.3.3.2 Product Portfolio 
 16.3.3.3 Financials
 16.3.3.4 SWOT Analysis
16.3.4 Biogen Inc.
 16.3.4.1 Company Overview
 16.3.4.2 Product Portfolio 
 16.3.4.3 Financials
 16.3.4.4 SWOT Analysis
16.3.5 Bristol Myers Squibb Company
 16.3.5.1 Company Overview
 16.3.5.2 Product Portfolio 
 16.3.5.3 Financials
 16.3.5.4 SWOT Analysis
16.3.6 F. Hoffmann-La Roche AG (Roche Holding AG)
 16.3.6.1 Company Overview
 16.3.6.2 Product Portfolio 
 16.3.6.3 SWOT Analysis
16.3.7 Jazz Pharmaceuticals Plc
 16.3.7.1 Company Overview
 16.3.7.2 Product Portfolio 
 16.3.7.3 Financials
 16.3.7.4 SWOT Analysis
16.3.8 Johnson & Johnson 
 16.3.8.1 Company Overview
 16.3.8.2 Product Portfolio
 16.3.8.3 Financials
 16.3.8.4 SWOT Analysis
16.3.9 Merck & Co. Inc.
 16.3.9.1 Company Overview
 16.3.9.2 Product Portfolio 
 16.3.9.3 Financials
 16.3.9.4 SWOT Analysis
16.3.10 Novartis AG
 16.3.10.1 Company Overview
 16.3.10.2 Product Portfolio 
 16.3.10.3 Financials
 16.3.10.4 SWOT Analysis
16.3.11 Pfizer Inc.
 16.3.11.1 Company Overview
 16.3.11.2 Product Portfolio 
 16.3.11.3 Financials
 16.3.11.4 SWOT Analysis
16.3.12 Sanofi S.A. 
 16.3.12.1 Company Overview
 16.3.12.2 Product Portfolio 
 16.3.12.3 Financials
 16.3.12.4 SWOT Analysis
16.3.13 Takeda Pharmaceutical Company Limited 
 16.3.13.1 Company Overview
 16.3.13.2 Product Portfolio 
 16.3.13.3 Financials
 16.3.13.4 SWOT Analysis
16.3.14 Teva Pharmaceutical Industries Ltd
 16.3.14.1 Company Overview
 16.3.14.2 Product Portfolio 
 16.3.14.3 Financials
 16.3.14.4 SWOT Analysis

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