Mucopolysaccharidosis II (MPS II) Marketed and Pipeline Drugs Assessment, Clinical Trials and Competitive Landscape

Mucopolysaccharidosis II (MPS II) Marketed and Pipeline Drugs Assessment, Clinical Trials and Competitive Landscape

Summary

This reports provides a data-driven overview of the current and future competitive landscape in MPH II therapeutics.

  • There will be more than 3,300 diagnosed prevalent cases of MPH-II in 2023 in the 16 major markets.
  • The marketed drugs space for MPS II include molecules targeting iduronate 2 sulfatase (IDS) replacement.
  • R&D activity within the MPS II space is significant, with four pipeline products in late-stage clinical development.
  • Commercial sponsors currently dominate the MPS II clinical development space, with South Korea and Japan as the emerging key countries for conducting Phase III trials in MPS II.
Scope

GlobalData’s Mucopolysaccharidosis II (MPS II) Marketed and Pipeline Drugs Assessment, Clinical Trials and Competitive Landscape combines data from the Pharma Intelligence Center with in-house analyst expertise to provide a competitive assessment of the disease marketplace.

Components of the report include -
  • Disease Landscape
  • Disease Overview
  • Epidemiology Overview
  • Treatment Overview
  • Marketed Products Assessment
  • Breakdown by Mechanism of Action, Molecule Type, Route of Administration
  • Product Profiles with Sales Forecast
  • Pricing and Reimbursement Assessment
  • Annual Therapy Cost
  • Time to Pricing and Time to Reimbursement
  • Pipeline Assessment
  • Breakdown by Development Stage, Mechanism of Action, Molecule Type, Route of Administration
  • Product Profiles with Sales Forecast
  • Late-to-mid-stage Pipeline Drugs
  • Phase Transition Success Rate and Likelihood of Approval
  • Clinical Trials Assessment
  • Breakdown of Trials by Phase, Status, Virtual Components, Sponsors, Geography, and Endpoint Status
  • Enrolment Analytics, Site Analytics, Feasibility Analysis
  • Deals Landscape
  • Mergers, Acquisitions, and Strategic Alliances by Region
  • Overview of Recent Deals
  • Commercial Assessment
  • Key Market Players
  • Future Market Catalysts
Reasons to Buy
  • Develop and design your in-licensing and out-licensing strategies through a review of pipeline products and technologies, and by identifying the companies with the most robust pipeline.
  • Develop business strategies by understanding the trends shaping and driving the MPH II market.
  • Drive revenues by understanding the key trends, innovative products and technologies, market segments, and companies likely to impact the global MPH II market in the future.
  • Formulate effective sales and marketing strategies by understanding the competitive landscape and by analyzing the performance of various competitors.
  • Identify emerging players with potentially strong product portfolios and create effective counter-strategies to gain a competitive advantage.
  • Organize your sales and marketing efforts by identifying the market categories and segments that present maximum opportunities for consolidations, investments, and strategic partnerships.


  • Key Findings
  • Disease Overview
  • Epidemiology Overview
    • Epidemiology Overview: Diagnosed Prevalent Cases of MPS II in 2023 and 2027
  • Treatment Overview
    • Treatment Guidelines
    • Treatment Algorithm for MPS II
  • Marketed Drugs Assessment
    • Marketed Drugs - Leading Marketed Drugs in MPS II
    • Marketed Drug Profile: JCR Pharmaceuticals’s Izcargo
    • Marketed Drug Profile: Takeda’s Elaprase
  • Pricing and Reimbursement Assessment
    • Marketed Drugs - Average Therapy Cost
    • Marketed Drugs - Time to Pricing and Reimbursement for Elaprase
  • Pipeline Drugs Assessment
    • Pipeline Drugs Overview - Mid-to-late-stage Pipeline Drugs in MPS II
    • Pipeline Drugs - Overview by Development Stage
    • Pipeline Drugs - Overview by Mechanism of Action
    • Pipeline Drugs - Drug-Specific Phase Transition Success Rate and Likelihood of Approval in MPS II
    • Pipeline Drugs - Phase Transition Success Rate and Likelihood of Approval in Rare Diseases.
  • Clinical Trials Assessment
    • Clinical Trials in MPS II - Historical Overview
    • Clinical Trials in MPS II - Overview by Phase
    • Clinical Trials in MPS II - Overview by Status
    • Clinical Trials in MPS II - Overview by Phase for Ongoing and Planned Trial
    • Clinical Trials in MPS II - Trials with a Virtual Component
    • Clinical Trials in MPS II - Geographic Overview
    • Clinical Trials in MPS II - Single-Country and Multinational Trials by Region
    • Clinical Trials in MPS II - Top 20 Sponsors with Breakdown by Phase
    • Clinical Trials in MPS II - Top 20 Sponsors with Breakdown by Status
    • Clinical Trials in MPS II - Enrollment Data
    • Clinical Trials in MPS II - Overview of Sites by Geography
    • Clinical Trials in MPS II - Top 10 Countries for Trial Sites
    • Clinical Trials in MPS II - Top 20 Sites Globally
    • Clinical Trials - Feasibility Analysis: Geography Overview
    • Clinical Trials - Feasibility Analysis: Benchmark Models for MPS II
  • Deals Landscape
    • Deals Landscape - Mergers, Acquisitions, and Strategic Alliances in MPS II by Region
    • Deals Landscape - Recent Mergers, Acquisitions, and Strategic Alliances in MPS II
  • Commercial Assessment
    • Commercial Assessment - Key Market Players in MPS II
  • Future Market Catalysts
    • Future Market Catalysts - Upcoming Market Catalysts in MPS II
  • Appendix
    • Methodology
    • Methodology - Sales Forecasts
    • Methodology - Pricing and Reimbursement
    • Methodology - Phase Transition Success Rate and Likelihood of Approval Analysis

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