Duchenne Muscular Dystrophy Drugs in Development by Stages, Target, MoA, RoA, Molecule Type and Key Players, 2022 Update

Duchenne Muscular Dystrophy Drugs in Development by Stages, Target, MoA, RoA, Molecule Type and Key Players, 2022 Update

Summary

Global Markets Direct's latest Pharmaceutical and Healthcare disease pipeline guide Duchenne Muscular Dystrophy - Drugs In Development, 2022, provides an overview of the Duchenne Muscular Dystrophy (Genetic Disorders) pipeline landscape.

Duchenne muscular dystrophy (DMD) is a genetic disorder that causes muscles to gradually weaken over time. Signs and symptoms of DMD include fatigue, learning difficulties, intellectual disability, muscle weakness and progressive difficulty walking. Risk factors include gender and family history. Treatment includes steroid medication, respiratory therapy and surgery.

Report Highlights

Global Markets Direct's Pharmaceutical and Healthcare latest pipeline guide Duchenne Muscular Dystrophy - Drugs In Development, 2022, provides comprehensive information on the therapeutics under development for Duchenne Muscular Dystrophy (Genetic Disorders), complete with analysis by stage of development, drug target, mechanism of action (MoA), route of administration (RoA) and molecule type. The guide covers the descriptive pharmacological action of the therapeutics, its complete research and development history and latest news and press releases.

The Duchenne Muscular Dystrophy (Genetic Disorders) pipeline guide also reviews of key players involved in therapeutic development for Duchenne Muscular Dystrophy and features dormant and discontinued projects. The guide covers therapeutics under Development by Companies /Universities /Institutes, the molecules developed by Companies in Pre-Registration, Filing rejected/Withdrawn, Phase III, Phase II, Phase I, IND/CTA Filed, Preclinical, Discovery and Unknown stages are 1, 1, 7, 12, 15, 2, 71, 34 and 1 respectively. Similarly, the Universities portfolio in Phase III, Phase II, Phase I, IND/CTA Filed, Preclinical and Discovery stages comprises 2, 1, 2, 1, 13 and 3 molecules, respectively.

Duchenne Muscular Dystrophy (Genetic Disorders) pipeline guide helps in identifying and tracking emerging players in the market and their portfolios, enhances decision making capabilities and helps to create effective counter strategies to gain competitive advantage. The guide is built using data and information sourced from Global Markets Direct’s proprietary databases, company/university websites, clinical trial registries, conferences, SEC filings, investor presentations and featured press releases from company/university sites and industry-specific third party sources. Additionally, various dynamic tracking processes ensure that the most recent developments are captured on a real time basis.

Note: Certain content / sections in the pipeline guide may be removed or altered based on the availability and relevance of data.

Scope

  • The pipeline guide provides a snapshot of the global therapeutic landscape of Duchenne Muscular Dystrophy (Genetic Disorders).
  • The pipeline guide reviews pipeline therapeutics for Duchenne Muscular Dystrophy (Genetic Disorders) by companies and universities/research institutes based on information derived from company and industry-specific sources.
  • The pipeline guide covers pipeline products based on several stages of development ranging from pre-registration till discovery and undisclosed stages.
  • The pipeline guide features descriptive drug profiles for the pipeline products which comprise, product description, descriptive licensing and collaboration details, R&D brief, MoA & other developmental activities.
  • The pipeline guide reviews key companies involved in Duchenne Muscular Dystrophy (Genetic Disorders) therapeutics and enlists all their major and minor projects.
  • The pipeline guide evaluates Duchenne Muscular Dystrophy (Genetic Disorders) therapeutics based on mechanism of action (MoA), drug target, route of administration (RoA) and molecule type.
  • The pipeline guide encapsulates all the dormant and discontinued pipeline projects.
  • The pipeline guide reviews latest news related to pipeline therapeutics for Duchenne Muscular Dystrophy (Genetic Disorders)
Reasons to Buy
  • Procure strategically important competitor information, analysis, and insights to formulate effective R&D strategies.
  • Recognize emerging players with potentially strong product portfolio and create effective counter-strategies to gain competitive advantage.
  • Find and recognize significant and varied types of therapeutics under development for Duchenne Muscular Dystrophy (Genetic Disorders).
  • Classify potential new clients or partners in the target demographic.
  • Develop tactical initiatives by understanding the focus areas of leading companies.
  • Plan mergers and acquisitions meritoriously by identifying key players and it’s most promising pipeline therapeutics.
  • Formulate corrective measures for pipeline projects by understanding Duchenne Muscular Dystrophy (Genetic Disorders) pipeline depth and focus of Indication therapeutics.
  • Develop and design in-licensing and out-licensing strategies by identifying prospective partners with the most attractive projects to enhance and expand business potential and scope.
  • Adjust the therapeutic portfolio by recognizing discontinued projects and understand from the know-how what drove them from pipeline.


Introduction
Global Markets Direct Report Coverage
Duchenne Muscular Dystrophy – Overview
Duchenne Muscular Dystrophy – Therapeutics Development
Pipeline Overview
Pipeline by Companies
Pipeline by Universities/Institutes
Products under Development by Companies
Products under Development by Universities/Institutes
Duchenne Muscular Dystrophy – Therapeutics Assessment
Assessment by Target
Assessment by Mechanism of Action
Assessment by Route of Administration
Assessment by Molecule Type
Duchenne Muscular Dystrophy – Companies Involved in Therapeutics Development
AAVogen Inc
Alpha Anomeric
American CryoStem Corp
Anagenesis Biotechnologies SAS
Antisense Therapeutics Ltd
ARMGO Pharma Inc
Astria Therapeutics Inc
AUM LifeTech Inc
Autotac Bio Inc
Avidity Biosciences Inc
Axolo Pharma Inc
Bayer AG
Biogen Inc
BioIncept LLC
Bioleaders Corp
BioMarin Pharmaceutical Inc
Biophytis SA
CANbridge Life Sciences Ltd
Capricor Therapeutics Inc
Chengdu Fanxi Biopharma Co Ltd
Code Biotherapeutics Inc
Consortium.AI
Constant Therapeutics LLC
CRISPR Therapeutics AG
Cumberland Pharmaceuticals Inc
Daiichi Sankyo Co Ltd
DepYmed Inc
DMD Therapeutics Inc
DTx Pharma Inc
Dyne Therapeutics Inc
Dystrogen Therapeutics SA
Edgewise Therapeutics Inc
Editas Medicine Inc
Eli Lilly and Co
Eloxx Pharmaceuticals Inc
Encell Co Ltd
Entrada Therapeutics Inc
Epirium Bio Inc
EryDel SpA
Evox Therapeutics Ltd
FibroGen Inc
FibroGenesis LLC
Fulcrum Therapeutics Inc
InnoBioscience LLC
Italfarmaco SpA
Ixchel Pharma LLC
J2H Biotech
Keros Therapeutics Inc
KSbitugen Co Ltd
LambdaGen Therapeutics
Ludi Therapeutics
Milo Biotechnology LLC
Mitobridge Inc
Mitochon Pharmaceuticals Inc
MitoRx Therapeutics Ltd
MyoGene Bio LLC
Myos Inc
Myosana Therapeutics Inc
MyoTherix Inc
Nippon Shinyaku Co Ltd
NS Pharma Inc
OliPass Corporation
OMEICOS Therapeutics GmbH
Oncocross Co Ltd
Oncotelic Inc
Pepgen Ltd
PeptiDream Inc
Pfizer Inc
Pharmaxis Ltd
PhaseBio Pharmaceuticals Inc
Pliant Therapeutics Inc
Progenitor Therapeutics Ltd
Prothelia Inc
PTC Therapeutics Inc
PYC Therapeutics Ltd
RASRx LLC
RegenxBio Inc
ReoStem LLC
Ridgeline Therapeutics LLC
Santhera Pharmaceuticals Holding AG
Sarcomed AB
Sarepta Therapeutics Inc
Satellos Bioscience Inc
Solid Biosciences Inc
Stealth BioTherapeutics Corp
SteroTherapeutics LLC
Sutura Therapeutics Ltd
Suzhou GenAssist Therapeutics Co Ltd
Taiho Pharmaceutical Co Ltd
Tivorsan Pharmaceuticals Inc
Tolerion Inc
Triplex Therapeutics Inc
UGISense AG
Ultragenyx Pharmaceutical Inc
Vandria SA
Vertex Pharmaceuticals Inc
Vita Therapeutics Inc
Wave Life Sciences Ltd
Zata Pharmaceuticals Inc
Duchenne Muscular Dystrophy – Drug Profiles
Anti-integrin mAb – Drug Profile
Product Description
Mechanism Of Action
Antisense Oligonucleotide 1 to Activate Dystrophin for Duchenne Muscular Dystrophy – Drug Profile
Product Description
Mechanism Of Action
History of Events
Antisense Oligonucleotide for Duchenne Muscular Dystrophy – Drug Profile
Product Description
Mechanism Of Action
-Antisense Oligonucleotide to Activate Dystrophin for Duchenne Muscular Dystrophy – Drug Profile
Product Description
Mechanism Of Action
History of Events
Antisense Oligonucleotide to Inhibit TGFB2 for Duchenne Muscular Dystrophy – Drug Profile
Product Description
Mechanism Of Action
Antisense Oligonucleotides for Duchenne Muscular Dystrophy – Drug Profile
Product Description
Mechanism Of Action
Antisense Oligonucleotides to Activate Dystrophin for Duchenne Muscular Dystrophy – Drug Profile
Product Description
Mechanism Of Action
Antisense RNAi Oligonucleotides for Duchenne Muscular Dystrophy – Drug Profile
Product Description
Mechanism Of Action
History of Events
AOC-1044 – Drug Profile
Product Description
Mechanism Of Action
AP-39 – Drug Profile
Product Description
Mechanism Of Action
ARM-210 – Drug Profile
Product Description
Mechanism Of Action
History of Events
ataluren – Drug Profile
Product Description
Mechanism Of Action
History of Events
ATC-401 – Drug Profile
Product Description
Mechanism Of Action
ATCell – Drug Profile
Product Description
Mechanism Of Action
ATL-1102 – Drug Profile
Product Description
Mechanism Of Action
History of Events
AVGN-7 – Drug Profile
Product Description
Mechanism Of Action
History of Events
BIIB-100 – Drug Profile
Product Description
Mechanism Of Action
History of Events
BIO-101 – Drug Profile
Product Description
Mechanism Of Action
History of Events
BLSM-22 – Drug Profile
Product Description
Mechanism Of Action
History of Events
BMN-351 – Drug Profile
Product Description
Mechanism Of Action
bocidelpar sulfate – Drug Profile
Product Description
Mechanism Of Action
History of Events
CAP-1002 – Drug Profile
Product Description
Mechanism Of Action
History of Events
CAP-2003 – Drug Profile
Product Description
Mechanism Of Action
History of Events
CAT-1041 – Drug Profile
Product Description
Mechanism Of Action
Cell Therapy for Duchenne Muscular Dystrophy – Drug Profile
Product Description
Mechanism Of Action
History of Events
CRISPR-Based Gene Therapy for Duchenne Muscular Dystrophy – Drug Profile
Product Description
Mechanism Of Action
CYMD-201 – Drug Profile
Product Description
Mechanism Of Action
delandistrogene moxeparvovec – Drug Profile
Product Description
Mechanism Of Action
History of Events
dexamethasone sodium phosphate – Drug Profile
Product Description
Mechanism Of Action
dextro epicatechin – Drug Profile
Product Description
Mechanism Of Action
History of Events
DMD-813 – Drug Profile
Product Description
Mechanism Of Action
Drug for Duchenne Muscular Dystrophy – Drug Profile
Product Description
Mechanism Of Action
DS-5144 – Drug Profile
Product Description
Mechanism Of Action
DS-5150 – Drug Profile
Product Description
Mechanism Of Action
DS-5151 – Drug Profile
Product Description
Mechanism Of Action
DS-5153 – Drug Profile
Product Description
Mechanism Of Action
DTDEC-01 – Drug Profile
Product Description
Mechanism Of Action
History of Events
Duchenne Muscular Dystrophy – Drug Profile
Product Description
Mechanism Of Action
EDG-5506 – Drug Profile
Product Description
Mechanism Of Action
EDG-6289 – Drug Profile
Product Description
Mechanism Of Action
elamipretide hydrochloride – Drug Profile
Product Description
Mechanism Of Action
History of Events
ELX-02 – Drug Profile
Product Description
Mechanism Of Action
History of Events
EN-001 – Drug Profile
Product Description
Mechanism Of Action
History of Events
ENTR-60144 – Drug Profile
Product Description
Mechanism Of Action
epicatechin – Drug Profile
Product Description
Mechanism Of Action
History of Events
eteplirsen – Drug Profile
Product Description
Mechanism Of Action
History of Events
finerenone – Drug Profile
Product Description
Mechanism Of Action
FNX-018 – Drug Profile
Product Description
Mechanism Of Action
FORCEM-23D – Drug Profile
Product Description
Mechanism Of Action
fordadistrogene movaparvovec – Drug Profile
Product Description
Mechanism Of Action
History of Events
Fusion Protein to Activate Utrophin for Duchenne Muscular Dystrophy – Drug Profile
Product Description
Mechanism Of Action
GEN-6045 – Drug Profile
Product Description
Mechanism Of Action
GEN-6050 – Drug Profile
Product Description
Mechanism Of Action
GEN-6051 – Drug Profile
Product Description
Mechanism Of Action
Gene Therapies to Activate Dystrophin for Duchenne Muscular Dystrophy – Drug Profile
Product Description
Mechanism Of Action
Gene Therapy 1 for Duchenne Muscular Dystrophy – Drug Profile
Product Description
Mechanism Of Action
History of Events
Gene Therapy 1 to Activate Dystrophin for Duchenne Muscular Dystrophy – Drug Profile
Product Description
Mechanism Of Action
History of Events
Gene therapy for Duchenne Muscular Dystrophy – Drug Profile
Product Description
Mechanism Of Action
Gene Therapy to Activate Dystrophin for Duchenne Muscular Dystrophy – Drug Profile
Product Description
Mechanism Of Action
History of Events
Gene therapy To Activate Follistatin For Duchenne Muscular Dystrophy, Facioscapulohumeral Muscular Dystrophy, Becker Muscular Dystrophy And Inclusion Body Myositis – Drug Profile
Product Description
Mechanism Of Action
History of Events
Gene Therapy to Activate GALGT2 for Duchenne Muscular Dystrophy – Drug Profile
Product Description
Mechanism Of Action
History of Events
Gene Therapy to Activate Utrophin for Duchenne Muscular Dystrophy – Drug Profile
Product Description
Mechanism Of Action
givinostat – Drug Profile
Product Description
Mechanism Of Action
History of Events
GNT-0004 – Drug Profile
Product Description
Mechanism Of Action
History of Events
golodirsen – Drug Profile
Product Description
Mechanism Of Action
History of Events
IB-DMD – Drug Profile
Product Description
Mechanism Of Action
ifetroban – Drug Profile
Product Description
Mechanism Of Action
History of Events
IXC-103 – Drug Profile
Product Description
Mechanism Of Action
IXC-109 – Drug Profile
Product Description
Mechanism Of Action
J-2H1803 – Drug Profile
Product Description
Mechanism Of Action
JAR-914 – Drug Profile
Product Description
Mechanism Of Action
KER-050 – Drug Profile
Product Description
Mechanism Of Action
History of Events
Kinase Derivatives – Drug Profile
Product Description
Mechanism Of Action
KSB-10201 – Drug Profile
Product Description
Mechanism Of Action
L-citrulline + metformin – Drug Profile
Product Description
Mechanism Of Action
History of Events
MA-0204 – Drug Profile
Product Description
Mechanism Of Action
History of Events
MG-53 – Drug Profile
Product Description
Mechanism Of Action
History of Events
MP-101 – Drug Profile
Product Description
Mechanism Of Action
MT-002 – Drug Profile
Product Description
Mechanism Of Action
Muscle Program – Drug Profile
Product Description
Mechanism Of Action
Myostatin antagonist – Drug Profile
Product Description
Mechanism Of Action
History of Events
nandrolone decanoate – Drug Profile
Product Description
Mechanism Of Action
History of Events
Next AOC DMD Programs-Exon 45 Dystrophin – Drug Profile
Product Description
Mechanism Of Action
Next AOC DMD Programs-Exon 51 Dystrophin – Drug Profile
Product Description
Mechanism Of Action
NS-045 – Drug Profile
Product Description
Mechanism Of Action
NS-050 – Drug Profile
Product Description
Mechanism Of Action
NS-051 – Drug Profile
Product Description
Mechanism Of Action
NS-055 – Drug Profile
Product Description
Mechanism Of Action
NS-089 – Drug Profile
Product Description
Mechanism Of Action
History of Events
OC-514 – Drug Profile
Product Description
Mechanism Of Action
Oligonucleotide for Duchenne Muscular Dystrophy – Drug Profile
Product Description
Mechanism Of Action
Oligonucleotide to Activate Dystrophin for Duchenne Muscular Dystrophy – Drug Profile
Product Description
Mechanism Of Action
OMT-28 – Drug Profile
Product Description
Mechanism Of Action
pamrevlumab – Drug Profile
Product Description
Mechanism Of Action
History of Events
PB-1023 – Drug Profile
Product Description
Mechanism Of Action
History of Events
PBGENE-DMD – Drug Profile
Product Description
Mechanism Of Action
History of Events
PGN-EDO45 – Drug Profile
Product Description
Mechanism Of Action
PGNEDO-44 – Drug Profile
Product Description
Mechanism Of Action
PGNEDO-51 – Drug Profile
Product Description
Mechanism Of Action
pizuglanstat – Drug Profile
Product Description
Mechanism Of Action
History of Events
Preimplantation Factor – Drug Profile
Product Description
Mechanism Of Action
History of Events
Protein for Duchenne Muscular Dystrophy – Drug Profile
Product Description
Mechanism Of Action
History of Events
Protein to Target Dystrophin for Duchenne Muscular Dystrophy – Drug Profile
Product Description
Mechanism Of Action
PXS-4699 – Drug Profile
Product Description
Mechanism Of Action
RASRx-1902 – Drug Profile
Product Description
Mechanism Of Action
History of Events
Recombinant Protein for Duchenne Muscular Dystrophy – Drug Profile
Product Description
Mechanism Of Action
renadirsen – Drug Profile
Product Description
Mechanism Of Action
History of Events
RGX-202 – Drug Profile
Product Description
Mechanism Of Action
History of Events
RHLAM-111 – Drug Profile
Product Description
Mechanism Of Action
History of Events
rimeporide – Drug Profile
Product Description
Mechanism Of Action
History of Events
RTC-13 – Drug Profile
Product Description
Mechanism Of Action
RTL-72484 – Drug Profile
Product Description
Mechanism Of Action
History of Events
SGT-001 – Drug Profile
Product Description
Mechanism Of Action
History of Events
SGT-003 – Drug Profile
Product Description
Mechanism Of Action
Small Molecule for Duchenne Muscular Dystrophy – Drug Profile
Product Description
Mechanism Of Action
Small Molecule to Activate UTRN for Duchenne Muscular Dystrophy – Drug Profile
Product Description
Mechanism Of Action
Small Molecule to Target Androgen Receptor and Glucocorticoid Receptor for Oncology, Autoimmune diseases and Inflammatory Disorders – Drug Profile
Product Description
Mechanism Of Action
Small Molecules for Duchenne Muscular Dystrophy – Drug Profile
Product Description
Mechanism Of Action
Small Molecules to Activate Utrophin for Duchenne Muscular Dystrophy – Drug Profile
Product Description
Mechanism Of Action
Small Molecules to Inhibit CLK for Solid Tumors and Duchenne Muscular Dystrophy – Drug Profile
Product Description
Mechanism Of Action
Small Molecules to Inhibit PGD2 Synthase for Asthma and Allergic Rhinitis – Drug Profile
Product Description
Mechanism Of Action
SRP-4044 – Drug Profile
Product Description
Mechanism Of Action
SRP-4050 – Drug Profile
Product Description
Mechanism Of Action
History of Events
SRP-4052 – Drug Profile
Product Description
Mechanism Of Action
SRP-4055 – Drug Profile
Product Description
Mechanism Of Action
SRP-5044 – Drug Profile
Product Description
Mechanism Of Action
SRP-5045 – Drug Profile
Product Description
Mechanism Of Action
SRP-5050 – Drug Profile
Product Description
Mechanism Of Action
SRP-5051 – Drug Profile
Product Description
Mechanism Of Action
History of Events
SRP-5052 – Drug Profile
Product Description
Mechanism Of Action
SRP-5053 – Drug Profile
Product Description
Mechanism Of Action
ST-002 – Drug Profile
Product Description
Mechanism Of Action
Stem Cell Therapy 1 to Activate Dystrophin for Duchenne Muscular Dystrophy – Drug Profile
Product Description
Mechanism Of Action
History of Events
Stem Cell Therapy 2 to Activate Dystrophin for Duchenne Muscular Dystrophy – Drug Profile
Product Description
Mechanism Of Action
History of Events
Stem Cell Therapy for Amyotrophic Lateral Sclerosis and Duchenne Muscular Dystrophy – Drug Profile
Product Description
Mechanism Of Action
History of Events
Stem Cell Therapy for Duchenne Muscular Dystrophy – Drug Profile
Product Description
Mechanism Of Action
History of Events
Stem Cell Therapy to Activate Dystrophin for Duchenne Muscular Dystrophy – Drug Profile
Product Description
Mechanism Of Action
SUT-001 – Drug Profile
Product Description
Mechanism Of Action
tamoxifen citrate – Drug Profile
Product Description
Mechanism Of Action
History of Events
testosterone – Drug Profile
Product Description
Mechanism Of Action
History of Events
trodusquemine – Drug Profile
Product Description
Mechanism Of Action
History of Events
TVN-102 – Drug Profile
Product Description
Mechanism Of Action
History of Events
TXA-127 – Drug Profile
Product Description
Mechanism Of Action
History of Events
Undisclosed-Duchenne Syndrome – Drug Profile
Product Description
Mechanism Of Action
History of Events
UX-810 – Drug Profile
Product Description
Mechanism Of Action
History of Events
vamorolone – Drug Profile
Product Description
Mechanism Of Action
History of Events
viltolarsen – Drug Profile
Product Description
Mechanism Of Action
History of Events
VTA-100 – Drug Profile
Product Description
Mechanism Of Action
History of Events
WVEN-531 – Drug Profile
Product Description
Mechanism Of Action
History of Events
X-0112 – Drug Profile
Product Description
Mechanism Of Action
Duchenne Muscular Dystrophy – Dormant Projects
Duchenne Muscular Dystrophy – Discontinued Products
Duchenne Muscular Dystrophy – Product Development Milestones
Featured News & Press Releases
Apr 28, 2022: Pfizer to open first U.S. sites in phase 3 trial of investigational gene therapy for ambulatory patients with Duchenne muscular dystrophy
Apr 07, 2022: Dystrogen Therapeutics investigational chimeric cell therapy DT-DEC01 for the treatment of Duchene Muscular Dystrophy shows safety and functional improvements
Apr 06, 2022: PepGen announces first participant dosed in a phase 1 clinical trial of PGN-EDO51 for the treatment of Duchenne Muscular Dystrophy
Mar 29, 2022: Santhera and ReveraGen start rolling NDA submission to the FDA for Vamorolone for the treatment of Duchenne Muscular Dystrophy
Mar 18, 2022: Exon 44-targeted DMD drug hits goals in PI/II: NCNP/Nippon Shinyaku
Mar 17, 2022: The result of an investigator-initiated clinical trial (First In Human trial) of NS-089/NCNP-02 for the treatment of Duchenne muscular dystrophy
Mar 16, 2022: Stealth BioTherapeutics showcases new Duchenne muscular dystrophy nonclinical data at the 2022 Muscular Dystrophy Association and Clinical Scientific Conference
Mar 15, 2022: PepGen announces approval by Health Canada of CTA to begin first in human trials of PGN-EDO51 to treat Duchenne Muscular Dystrophy
Mar 15, 2022: Santhera and ReveraGen to present efficacy and safety data with vamorolone at 2022 Muscular Dystrophy Association Conference
Mar 14, 2022: Significant modulation of two bone morphogenetic proteins supports potential of ATL1102 for improving bone density in DMD
Mar 11, 2022: The Lancet publishes positive results from Capricor Therapeutics’ phase 2 study evaluating CAP-1002 in late-stage Duchenne muscular dystrophy
Mar 11, 2022: The result of an investigator-initiated clinical trial (First In Human trial) of NS-089/NCNP-02 for the treatment of Duchenne muscular dystrophy
Mar 09, 2022: Antisense Therapeutics to present poster at world’s largest NMD conference
Mar 08, 2022: Edgewise Therapeutics to present on EDG-5506 for Becker and Duchenne Muscular Dystrophy (BMD, DMD) at the 2022 Annual MDA Clinical and Scientific Conference
Mar 08, 2022: Roche to present new SRP-9001 data at MDA 2022 and highlight expanding neuromuscular disease portfolio
Appendix
Methodology
Coverage
Secondary Research
Primary Research
Expert Panel Validation
Contact Us
Disclaimer
List of Tables
Table 1: Number of Products under Development for Duchenne Muscular Dystrophy, 2022
Table 2: Number of Products under Development by Companies, 2022
Table 3: Number of Products under Development by Companies, 2022 (Contd..1)
Table 4: Number of Products under Development by Companies, 2022 (Contd..2)
Table 5: Number of Products under Development by Companies, 2022 (Contd..3)
Table 6: Number of Products under Development by Companies, 2022 (Contd..4)
Table 7: Number of Products under Development by Universities/Institutes, 2022
Table 8: Products under Development by Companies, 2022
Table 9: Products under Development by Companies, 2022 (Contd..1)
Table 10: Products under Development by Companies, 2022 (Contd..2)
Table 11: Products under Development by Companies, 2022 (Contd..3)
Table 12: Products under Development by Companies, 2022 (Contd..4)
Table 13: Products under Development by Companies, 2022 (Contd..5)
Table 14: Products under Development by Companies, 2022 (Contd..6)
Table 15: Products under Development by Companies, 2022 (Contd..7)
Table 16: Products under Development by Companies, 2022 (Contd..8)
Table 17: Products under Development by Universities/Institutes, 2022
Table 18: Number of Products by Stage and Target, 2022
Table 19: Number of Products by Stage and Target, 2022 (Contd..1)
Table 20: Number of Products by Stage and Mechanism of Action, 2022
Table 21: Number of Products by Stage and Mechanism of Action, 2022 (Contd..1)
Table 22: Number of Products by Stage and Route of Administration, 2022
Table 23: Number of Products by Stage and Molecule Type, 2022
Table 24: Duchenne Muscular Dystrophy – Pipeline by AAVogen Inc, 2022
Table 25: Duchenne Muscular Dystrophy – Pipeline by Alpha Anomeric, 2022
Table 26: Duchenne Muscular Dystrophy – Pipeline by American CryoStem Corp, 2022
Table 27: Duchenne Muscular Dystrophy – Pipeline by Anagenesis Biotechnologies SAS, 2022
Table 28: Duchenne Muscular Dystrophy – Pipeline by Antisense Therapeutics Ltd, 2022
Table 29: Duchenne Muscular Dystrophy – Pipeline by ARMGO Pharma Inc, 2022
Table 30: Duchenne Muscular Dystrophy – Pipeline by Astria Therapeutics Inc, 2022
Table 31: Duchenne Muscular Dystrophy – Pipeline by AUM LifeTech Inc, 2022
Table 32: Duchenne Muscular Dystrophy – Pipeline by Autotac Bio Inc, 2022
Table 33: Duchenne Muscular Dystrophy – Pipeline by Avidity Biosciences Inc, 2022
Table 34: Duchenne Muscular Dystrophy – Pipeline by Axolo Pharma Inc, 2022
Table 35: Duchenne Muscular Dystrophy – Pipeline by Bayer AG, 2022
Table 36: Duchenne Muscular Dystrophy – Pipeline by Biogen Inc, 2022
Table 37: Duchenne Muscular Dystrophy – Pipeline by BioIncept LLC, 2022
Table 38: Duchenne Muscular Dystrophy – Pipeline by Bioleaders Corp, 2022
Table 39: Duchenne Muscular Dystrophy – Pipeline by BioMarin Pharmaceutical Inc, 2022
Table 40: Duchenne Muscular Dystrophy – Pipeline by Biophytis SA, 2022
Table 41: Duchenne Muscular Dystrophy – Pipeline by CANbridge Life Sciences Ltd, 2022
Table 42: Duchenne Muscular Dystrophy – Pipeline by Capricor Therapeutics Inc, 2022
Table 43: Duchenne Muscular Dystrophy – Pipeline by Chengdu Fanxi Biopharma Co Ltd, 2022
Table 44: Duchenne Muscular Dystrophy – Pipeline by Code Biotherapeutics Inc, 2022
Table 45: Duchenne Muscular Dystrophy – Pipeline by Consortium.AI, 2022
Table 46: Duchenne Muscular Dystrophy – Pipeline by Constant Therapeutics LLC, 2022
Table 47: Duchenne Muscular Dystrophy – Pipeline by CRISPR Therapeutics AG, 2022
Table 48: Duchenne Muscular Dystrophy – Pipeline by Cumberland Pharmaceuticals Inc, 2022
Table 49: Duchenne Muscular Dystrophy – Pipeline by Daiichi Sankyo Co Ltd, 2022
Table 50: Duchenne Muscular Dystrophy – Pipeline by DepYmed Inc, 2022
Table 51: Duchenne Muscular Dystrophy – Pipeline by DMD Therapeutics Inc, 2022
Table 52: Duchenne Muscular Dystrophy – Pipeline by DTx Pharma Inc, 2022
Table 53: Duchenne Muscular Dystrophy – Pipeline by Dyne Therapeutics Inc, 2022
Table 54: Duchenne Muscular Dystrophy – Pipeline by Dystrogen Therapeutics SA, 2022
Table 55: Duchenne Muscular Dystrophy – Pipeline by Edgewise Therapeutics Inc, 2022
Table 56: Duchenne Muscular Dystrophy – Pipeline by Editas Medicine Inc, 2022
Table 57: Duchenne Muscular Dystrophy – Pipeline by Eli Lilly and Co, 2022
Table 58: Duchenne Muscular Dystrophy – Pipeline by Eloxx Pharmaceuticals Inc, 2022
Table 59: Duchenne Muscular Dystrophy – Pipeline by Encell Co Ltd, 2022
Table 60: Duchenne Muscular Dystrophy – Pipeline by Entrada Therapeutics Inc, 2022
Table 61: Duchenne Muscular Dystrophy – Pipeline by Epirium Bio Inc, 2022
Table 62: Duchenne Muscular Dystrophy – Pipeline by EryDel SpA, 2022
Table 63: Duchenne Muscular Dystrophy – Pipeline by Evox Therapeutics Ltd, 2022
Table 64: Duchenne Muscular Dystrophy – Pipeline by FibroGen Inc, 2022
Table 65: Duchenne Muscular Dystrophy – Pipeline by FibroGenesis LLC, 2022
Table 66: Duchenne Muscular Dystrophy – Pipeline by Fulcrum Therapeutics Inc, 2022
Table 67: Duchenne Muscular Dystrophy – Pipeline by InnoBioscience LLC, 2022
Table 68: Duchenne Muscular Dystrophy – Pipeline by Italfarmaco SpA, 2022
Table 69: Duchenne Muscular Dystrophy – Pipeline by Ixchel Pharma LLC, 2022
Table 70: Duchenne Muscular Dystrophy – Pipeline by J2H Biotech, 2022
Table 71: Duchenne Muscular Dystrophy – Pipeline by Keros Therapeutics Inc, 2022
Table 72: Duchenne Muscular Dystrophy – Pipeline by KSbitugen Co Ltd, 2022
Table 73: Duchenne Muscular Dystrophy – Pipeline by LambdaGen Therapeutics, 2022
Table 74: Duchenne Muscular Dystrophy – Pipeline by Ludi Therapeutics, 2022
Table 75: Duchenne Muscular Dystrophy – Pipeline by Milo Biotechnology LLC, 2022
Table 76: Duchenne Muscular Dystrophy – Pipeline by Mitobridge Inc, 2022
Table 77: Duchenne Muscular Dystrophy – Pipeline by Mitochon Pharmaceuticals Inc, 2022
Table 78: Duchenne Muscular Dystrophy – Pipeline by MitoRx Therapeutics Ltd, 2022
Table 79: Duchenne Muscular Dystrophy – Pipeline by MyoGene Bio LLC, 2022
Table 80: Duchenne Muscular Dystrophy – Pipeline by Myos Inc, 2022
Table 81: Duchenne Muscular Dystrophy – Pipeline by Myosana Therapeutics Inc, 2022
Table 82: Duchenne Muscular Dystrophy – Pipeline by MyoTherix Inc, 2022
Table 83: Duchenne Muscular Dystrophy – Pipeline by Nippon Shinyaku Co Ltd, 2022
Table 84: Duchenne Muscular Dystrophy – Pipeline by NS Pharma Inc, 2022
Table 85: Duchenne Muscular Dystrophy – Pipeline by OliPass Corporation, 2022
Table 86: Duchenne Muscular Dystrophy – Pipeline by OMEICOS Therapeutics GmbH, 2022
Table 87: Duchenne Muscular Dystrophy – Pipeline by Oncocross Co Ltd, 2022
Table 88: Duchenne Muscular Dystrophy – Pipeline by Oncotelic Inc, 2022
Table 89: Duchenne Muscular Dystrophy – Pipeline by Pepgen Ltd, 2022
Table 90: Duchenne Muscular Dystrophy – Pipeline by PeptiDream Inc, 2022
Table 91: Duchenne Muscular Dystrophy – Pipeline by Pfizer Inc, 2022
Table 92: Duchenne Muscular Dystrophy – Pipeline by Pharmaxis Ltd, 2022
Table 93: Duchenne Muscular Dystrophy – Pipeline by PhaseBio Pharmaceuticals Inc, 2022
Table 94: Duchenne Muscular Dystrophy – Pipeline by Pliant Therapeutics Inc, 2022
Table 95: Duchenne Muscular Dystrophy – Pipeline by Progenitor Therapeutics Ltd, 2022
Table 96: Duchenne Muscular Dystrophy – Pipeline by Prothelia Inc, 2022
Table 97: Duchenne Muscular Dystrophy – Pipeline by PTC Therapeutics Inc, 2022
Table 98: Duchenne Muscular Dystrophy – Pipeline by PYC Therapeutics Ltd, 2022
Table 99: Duchenne Muscular Dystrophy – Pipeline by RASRx LLC, 2022
Table 100: Duchenne Muscular Dystrophy – Pipeline by RegenxBio Inc, 2022
Table 101: Duchenne Muscular Dystrophy – Pipeline by ReoStem LLC, 2022
Table 102: Duchenne Muscular Dystrophy – Pipeline by Ridgeline Therapeutics LLC, 2022
Table 103: Duchenne Muscular Dystrophy – Pipeline by Santhera Pharmaceuticals Holding AG, 2022
Table 104: Duchenne Muscular Dystrophy – Pipeline by Sarcomed AB, 2022
Table 105: Duchenne Muscular Dystrophy – Pipeline by Sarepta Therapeutics Inc, 2022
Table 106: Duchenne Muscular Dystrophy – Pipeline by Satellos Bioscience Inc, 2022
Table 107: Duchenne Muscular Dystrophy – Pipeline by Solid Biosciences Inc, 2022
Table 108: Duchenne Muscular Dystrophy – Pipeline by Stealth BioTherapeutics Corp, 2022
Table 109: Duchenne Muscular Dystrophy – P

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