Aplastic Anemia - Pipeline Insight, 2024

Aplastic Anemia - Pipeline Insight, 2024



DelveInsight’s, “Aplastic Anemia - Pipeline Insight, 2024,” report provides comprehensive insights about 8+ companies and 8+ pipeline drugs in Aplastic Anemia pipeline landscape. It covers the pipeline drug profiles, including clinical and nonclinical stage products. It also covers the therapeutics assessment by product type, stage, route of administration, and molecule type. It further highlights the inactive pipeline products in this space.

Geography Covered
  • Global coverage
Aplastic Anemia Understanding

Aplastic Anemia: Overview

Aplastic anemia (AA) is a life-threatening form of bone marrow failure which, if untreated, is associated with very high mortality. AA refers to pancytopenia in association with bone marrow hypoplasia/aplasia, most often due to immune injury to multipotent hematopoietic stem cells. Aplastic anemia can be moderate, severe or very severe. People with severe or very severe aplastic anemia are at risk for life-threatening infections or bleeding. With prompt and proper care, most people who have aplastic anemia can be successfully treated. The only cure for aplastic anemia is a bone marrow transplant. Aplastic anemia can strike at any age regardless of race or gender. However, it is diagnosed more often in children, young adults and older adults. It also appears more often in Asian-Americans. Each year, between 600 and 900 people in the U.S. learn that they have aplastic anemia.

""Aplastic Anemia - Pipeline Insight, 2024"" report by DelveInsight outlays comprehensive insights of present scenario and growth prospects across the indication. A detailed picture of the Aplastic Anemia pipeline landscape is provided which includes the disease overview and Aplastic Anemia treatment guidelines. The assessment part of the report embraces, in depth Aplastic Anemia commercial assessment and clinical assessment of the pipeline products under development. In the report, detailed description of the drug is given which includes mechanism of action of the drug, clinical studies, NDA approvals (if any), and product development activities comprising the technology, Aplastic Anemia collaborations, licensing, mergers and acquisition, funding, designations and other product related details.

Report Highlights
  • The companies and academics are working to assess challenges and seek opportunities that could influence Aplastic Anemia R&D. The therapies under development are focused on novel approaches to treat/improve Aplastic Anemia.
Aplastic Anemia Emerging Drugs Chapters

This segment of the Aplastic Anemia report encloses its detailed analysis of various drugs in different stages of clinical development, including phase II, I, preclinical and Discovery. It also helps to understand clinical trial details, expressive pharmacological action, agreements and collaborations, and the latest news and press releases.

Aplastic Anemia Emerging Drugs
  • PF-06462700: Pfizer
PF-06462700 is an immunosuppressant/immunosuppressive agent. PF-06462700 is being developed by Pfizer for Aplastic Anemia patients and is currently in the phase III stage of development.
  • REGN7257: Regeneron Pharmaceuticals
REGN7257is being developed by Regeneron Pharmaceuticals for Aplastic Anemia. It is currently in phase I/II stage of development.
  • BL-8040: BioLineRx, Ltd.
BL-8040 (Motixafortide) targets CXCR4, a chemokine receptor and a well-validated therapeutic target that is over-expressed in many human cancers, including PDAC. CXCR4 plays a key role in tumor growth, invasion, angiogenesis, metastasis, therapeutic resistance, and CXCR4 overexpression correlated with poor prognosis. A Phase II clinical trial has been completed for BL-8040 for the treatment of Aplastic Anemia.

Further product details are provided in the report……..

Aplastic Anemia: Therapeutic Assessment

This segment of the report provides insights about the different Aplastic Anemia drugs segregated based on following parameters that define the scope of the report, such as:
  • Major Players in Aplastic Anemia
There are approx. 8+ key companies which are developing the therapies for Aplastic Anemia. The companies which have their Aplastic Anemia drug candidates in the most advanced stage, i.e. phase III include, Pfizer.
  • Phases
DelveInsight’s report covers around 8+ products under different phases of clinical development like
  • Late stage products (Phase III)
  • Mid-stage products (Phase II)
  • Early-stage product (Phase I) along with the details of
  • Pre-clinical and Discovery stage candidates
  • Discontinued & Inactive candidates
  • Route of Administration
Aplastic Anemia pipeline report provides the therapeutic assessment of the pipeline drugs by the Route of Administration. Products have been categorized under various ROAs such as
  • Oral
  • Parenteral
  • intravenous
  • Subcutaneous
  • Topical.
  • Molecule Type
Products have been categorized under various Molecule types such as
  • Monoclonal Antibody
  • Peptides
  • Polymer
  • Small molecule
  • Gene therapy
  • Product Type
Drugs have been categorized under various product types like Mono, Combination and Mono/Combination.

Aplastic Anemia: Pipeline Development Activities

The report provides insights into different therapeutic candidates in phase II, I, preclinical and discovery stage. It also analyses Aplastic Anemia therapeutic drugs key players involved in developing key drugs.

Pipeline Development Activities

The report covers the detailed information of collaborations, acquisition and merger, licensing along with a thorough therapeutic assessment of emerging Aplastic Anemia drugs.

Aplastic Anemia Report Insights
  • Aplastic Anemia Pipeline Analysis
  • Therapeutic Assessment
  • Unmet Needs
  • Impact of Drugs
Aplastic Anemia Report Assessment
  • Pipeline Product Profiles
  • Therapeutic Assessment
  • Pipeline Assessment
  • Inactive drugs assessment
  • Unmet Needs
Key Questions

Current Treatment Scenario and Emerging Therapies:
  • How many companies are developing Aplastic Anemia drugs?
  • How many Aplastic Anemia drugs are developed by each company?
  • How many emerging drugs are in mid-stage, and late-stage of development for the treatment of Aplastic Anemia?
  • What are the key collaborations (Industry–Industry, Industry–Academia), Mergers and acquisitions, licensing activities related to the Aplastic Anemia therapeutics?
  • What are the recent trends, drug types and novel technologies developed to overcome the limitation of existing therapies?
  • What are the clinical studies going on for Aplastic Anemia and their status?
  • What are the key designations that have been granted to the emerging drugs?
Key Players
  • Pfizer
  • BioLineRx, Ltd.
  • Regeneron Pharmaceuticals
  • Gamida Cell
  • Elixirgen
  • Hangzhou Zede Pharmaceutical Technology
  • Cellenkos
  • Hemogenyx Pharmaceuticals
Key Products
  • PF-06462700
  • BL-8040
  • REGN7257
  • Omidubicel
  • EXG 34217
  • CN 128
  • CK0801
  • Hu-PHEC Liver


Introduction
Executive Summary
Aplastic Anemia: Overview
Causes
Mechanism of Action
Signs and Symptoms
Diagnosis
Disease Management
Pipeline Therapeutics
Comparative Analysis
Therapeutic Assessment
Assessment by Product Type
Assessment by Stage and Product Type
Assessment by Route of Administration
Assessment by Stage and Route of Administration
Assessment by Molecule Type
Assessment by Stage and Molecule Type
Aplastic Anemia – DelveInsight’s Analytical Perspective
Late Stage Products (Phase III)
Comparative Analysis
PF-06462700: Pfizer
Product Description
Research and Development
Product Development Activities
Drug profiles in the detailed report…..
Mid Stage Products (Phase II)
Comparative Analysis
BL-8040: BioLineRx, Ltd.
Product Description
Research and Development
Product Development Activities
Drug profiles in the detailed report…..
Early Stage Products (Phase I/II)
Comparative Analysis
REGN7257: Regeneron Pharmaceuticals
Product Description
Research and Development
Product Development Activities
Drug profiles in the detailed report…..
Inactive Products
Comparative Analysis
Aplastic Anemia Key Companies
Aplastic Anemia Key Products
Aplastic Anemia- Unmet Needs
Aplastic Anemia- Market Drivers and Barriers
Aplastic Anemia- Future Perspectives and Conclusion
Aplastic Anemia Analyst Views
Aplastic Anemia Key Companies
Appendix

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