North America Sickle Cell Disease Market, By Disease Type (Sickle Cell Anemia, Sickle Beta Thalassemia, Sickle Hemoglobin C Disease), By Drug Type (Hydroxyurea, L-glutamine, Crizanlizumab, Pain-relievers, Voxelotor, Others), By Distribution Channel (Hospi
North America Sickle Cell Disease Market, By Disease Type (Sickle Cell Anemia, Sickle Beta Thalassemia, Sickle Hemoglobin C Disease), By Drug Type (Hydroxyurea, L-glutamine, Crizanlizumab, Pain-relievers, Voxelotor, Others), By Distribution Channel (Hospital Pharmacies, Retail Pharmacies, Online Pharmacies)
Sickle Cell Disease (SCD) is a group of inherited red blood cell disorders. Red blood cells contain hemoglobin, a protein that carries oxygen. Healthy red blood cells are round, and they move through small blood vessels to carry oxygen to all parts of the body. In someone who has SCD, the hemoglobin is abnormal, which causes the red blood cells to become hard and sticky and look like a C-shaped farm tool called a “sickle.” Sickle cells die early, which causes a constant shortage of red blood cells. Also, when they travel through small blood vessels, they get stuck and clog the blood flow. This can cause pain and other serious complications (health problems) such as infection, acute chest syndrome, and stroke. Thus, the introduction of advanced products in the market is expected to drive the growth of the North America sickle cell disease market over the forecast period.
Market Dynamics
The key players in the pharmaceutical industry are focusing on the development of technologically advanced drugs for the treatment of sickle cell disease. Thus, the introduction of such advanced products in the market is expected to the drive growth of the North America sickle cell disease market over the forecast period. F006F r instance, on June 21, 2023, bluebird bio, Inc., a biotechnology company, announced that the U.S. Food and Drug Administration (FDA) has accepted the Biologics License Application (BLA) for lovotibeglogene autotemcel (lovo-cel) for priority review. Lovo-cel is a potentially transformative one-time gene therapy for individuals living with Sickle Cell Disease (SCD) for ages 12 and older who have a history of Vaso-occlusive Events (VOEs). It is specifically designed to treat the underlying cause of SCD through the addition of a functional gene that enables the production of anti-sickling adult hemoglobin and is the most deeply studied gene therapy in development for this disease.
Key features of the study:
This report provides an in-depth analysis of the North America sickle cell disease market and provides market size (US$ Million) and Compound Annual Growth rate (CAGR) for the forecast period (2023-2030), considering 2022 as the base year
It elucidates potential revenue growth opportunities across different segments and explains attractive investment proposition matrices for this market
This study also provides key insights about market drivers, restraints, opportunities, new product launches or approvals, market trends, regional outlook, and competitive strategies adopted by key players
It profiles key players in the North America sickle cell disease market based on the following parameters - company highlights, products portfolio, key highlights, financial performance, and strategies
The key companies covered as a part of this study include Novartis International AG, Bristol-Myers Squibb Company, Global Blood Therapeutics, Inc., Pfizer Inc., Emmaus Life Sciences, Inc., ADDMEDICA, Sangamo Therapeutics, Inc., Acceleron Pharma, Inc., Agios Pharmaceuticals, Inc., Chiesi Farmaceutici S.p.A., Vertex Pharmaceuticals, Inc., IMARA, , bluebird bio, Inc., CRISPR Therapeutics, Scribe Therapeutics Inc., Fulcrum Therapeutics, Inc., HPC International, Editas Medicine, Inc., Nicox SA, Fera Pharmaceuticals, and Tessera Therapeutics
Insights from this report would allow marketers and the management authorities of the companies to make informed decisions regarding their future product launches, type up-gradation, market expansion, and marketing tactics
The North America sickle cell disease market report caters to various stakeholders in this industry including investors, suppliers, product manufacturers, distributors, new entrants, and financial analysts
Stakeholders would have ease in decision-making through various strategy matrices used in analyzing the North America sickle cell disease market
Detailed Segmentation:
By Disease Type:
Sickle Cell Anemia
Sickle Beta Thalassemia
Sickle Hemoglobin C Disease
By Drug Type:
Hydroxyurea
L-glutamine
Crizanlizumab
Pain-relievers
Voxelotor
Others
By Distribution Channel:
Hospital Pharmacies
Retail Pharmacies
Online Pharmacies
By Country:
U.S.
Canada
Company Profiles
Novartis International AG
Bristol-Myers Squibb Company
Global Blood Therapeutics, Inc.
Pfizer Inc.
Emmaus Life Sciences, Inc.
ADDMEDICA
Sangamo Therapeutics, Inc.
Acceleron Pharma, Inc.
Agios Pharmaceuticals, Inc.
Chiesi Farmaceutici S.p.A.
Vertex Pharmaceuticals, Inc.
IMARA, Inc.
bluebird bio, Inc.
CRISPR Therapeutics
Scribe Therapeutics Inc.
Fulcrum Therapeutics, Inc.
HPC International
Editas Medicine, Inc.
Nicox SA
Fera Pharmaceuticals
Tessera Therapeutics
1. Research Objective and Assumption
Research Objectives
Assumptions
Abbreviations
2. Market Purview
Report Description
Market Definition and Scope
Executive Summary
Market Snippet, By Disease Type
Market Snippet, By Drug Type
Market Snippet, By Distribution Channel
Market Snippet, By Country
Coherent Opportunity Map (COM)
3. Market Dynamics, Regulations, and Trends Analysis
Market Dynamics
Drivers
Restraints
Market Opportunities
Impact Analysis
Recent Test Launches
Epidemiology
Merger, Acquisition, and Collaborations
Regulatory Scenario
Key Developments
PEST Analysis
PORTER’S Analysis
Pipeline Analysis
4. North America Sickle Cell Disease Market - COVID-19 Impact Analysis
Economic Impact
COVID-19 Epidemiology
Impact on Supply and Demand
5. North America Sickle Cell Disease Market, By Disease Type, 2018-2030, (US$ Mn)
Introduction
Market Share Analysis, 2023 and 2030 (%)
Y-o-Y Growth Analysis, 2018-2030
Segment Trends
Sickle Cell Anemia
Introduction
Market Size and Forecast, and Y-o-Y Growth, 2018-2030, (US$ Mn)
Segment Trends
Sickle Beta Thalassemia
Introduction
Market Size and Forecast, and Y-o-Y Growth, 2018-2030, (US$ Mn)
Segment Trends
Sickle Hemoglobin C Disease
Introduction
Market Size and Forecast, and Y-o-Y Growth, 2018-2030, (US$ Mn)
Segment Trends
6. North America Sickle Cell Disease Market, By Drug Type, 2018-2030, (US$ Mn)
Introduction
Market Share Analysis, 2023 and 2030 (%)
Y-o-Y Growth Analysis, 2018-2030
Segment Trends
Hydroxyurea
Introduction
Market Size and Forecast, and Y-o-Y Growth, 2018-2030, (US$ Mn)
Segment Trends
L-glutamine
Introduction
Market Size and Forecast, and Y-o-Y Growth, 2018-2030, (US$ Mn)
Segment Trends
Crizanlizumab
Introduction
Market Size and Forecast, and Y-o-Y Growth, 2018-2030, (US$ Mn)
Segment Trends
Pain-relievers
Introduction
Market Size and Forecast, and Y-o-Y Growth, 2018-2030, (US$ Mn)
Segment Trends
Voxelotor
Introduction
Market Size and Forecast, and Y-o-Y Growth, 2018-2030, (US$ Mn)
Segment Trends
Others
Introduction
Market Size and Forecast, and Y-o-Y Growth, 2018-2030, (US$ Mn)
Segment Trends
7. North America Sickle Cell Disease Market, By Distribution Channel, 2018-2030, (US$ Mn)
Introduction
Market Share Analysis, 2023 and 2030 (%)
Y-o-Y Growth Analysis, 2018-2030
Segment Trends
Hospital Pharmacies
Introduction
Market Size and Forecast, and Y-o-Y Growth, 2018-2030, (US$ Mn)
Retail Pharmacies
Introduction
Market Size and Forecast, and Y-o-Y Growth, 2018-2030, (US$ Mn)
Online Pharmacies
Introduction
Market Size and Forecast, and Y-o-Y Growth, 2018-2030, (US$ Mn)
8. North America Sickle Cell Disease Market, By Country, 2018-2030, (US$ Mn)
Introduction
Market Share Analysis, 2023 and 2030 (%)
Y-o-Y Growth Analysis, 2018-2030
Segment Trends
U.S.
Introduction
Market Size and Forecast, Y-o-Y Growth and By Drug Type, 2018-2030, (US$ Mn)
Market Size and Forecast, Y-o-Y Growth and By Disease Type, 2018-2030, (US$ Mn)
Market Size and Forecast, Y-o-Y Growth and By Distribution Channel, 2018-2030, (US$ Mn)
Canada
Introduction
Market Size and Forecast, Y-o-Y Growth and By Drug Type, 2018-2030, (US$ Mn)
Market Size and Forecast, Y-o-Y Growth and By Disease Type, 2018-2030, (US$ Mn)
Market Size and Forecast, Y-o-Y Growth and By Distribution Channel, 2018-2030, (US$ Mn)
9. Competitive Landscape
Company Profiles
Novartis International AG*
Company Overview
Product Portfolio
Key Highlights
Financial Overview
Strategies
Bristol-Myers Squibb Company
Company Overview
Product Portfolio
Key Highlights
Financial Overview
Strategies
Global Blood Therapeutics, Inc.
Company Overview
Product Portfolio
Key Highlights
Financial Overview
Strategies
Pfizer Inc.
Company Overview
Product Portfolio
Key Highlights
Financial Overview
Strategies
Emmaus Life Sciences, Inc.
Company Overview
Product Portfolio
Key Highlights
Financial Overview
Strategies
ADDMEDICA
Company Overview
Product Portfolio
Key Highlights
Financial Overview
Strategies
Sangamo Therapeutics, Inc.
Company Overview
Product Portfolio
Key Highlights
Financial Overview
Strategies
Acceleron Pharma, Inc.
Company Overview
Product Portfolio
Key Highlights
Financial Overview
Strategies
Agios Pharmaceuticals, Inc.
Company Overview
Product Portfolio
Key Highlights
Financial Overview
Strategies
Chiesi Farmaceutici S.p.A.
Company Overview
Product Portfolio
Key Highlights
Financial Overview
Strategies
Vertex Pharmaceuticals, Inc.
Company Overview
Product Portfolio
Key Highlights
Financial Overview
Strategies
IMARA, Inc.
Company Overview
Product Portfolio
Key Highlights
Financial Overview
Strategies
CRISPR Therapeutics
Company Overview
Product Portfolio
Key Highlights
Financial Overview
Strategies
Scribe Therapeutics Inc.
Company Overview
Product Portfolio
Key Highlights
Financial Overview
Strategies
Fulcrum Therapeutics, Inc.
Company Overview
Product Portfolio
Key Highlights
Financial Overview
Strategies
HPC International
Company Overview
Product Portfolio
Key Highlights
Financial Overview
Strategies
Editas Medicine, Inc.
Company Overview
Product Portfolio
Key Highlights
Financial Overview
Strategies
Nicox SA
Company Overview
Product Portfolio
Key Highlights
Financial Overview
Strategies
Fera Pharmaceuticals
Company Overview
Product Portfolio
Key Highlights
Financial Overview
Strategies
Tessera Therapeutics
Company Overview
Product Portfolio
Key Highlights
Financial Overview
Strategies
10. Section
References
Research Methodology
About us and Sales Contact
*Browse 17 market data tables and 24 figures on “North America Sickle Cell Disease Market” – North America forecast to 2030