Hemoglobinopathy Treatment Drugs Market

Hemoglobinopathy Treatment Drugs Market, By Drug Type, By Disease Type, By Distribution Channel, By Region (North America, Latin America, Europe, Asia Pacific, Middle East, and Africa) -Size, Share, Outlook, and Opportunity Analysis, 2023 - 2030


The hemoglobinopathies encompass all genetic diseases of hemoglobin. They fall into two main groups: thalassemia syndromes and structural hemoglobin variants (abnormal hemoglobins). α and β thalassemia are the main types of thalassemia; the main structural hemoglobin variants are HbS, HbE, and HbC. There are many subtypes and combined types in each group. The highly variable clinical manifestations of the hemoglobinopathies range from mild hypochromic anemia to moderate hematological disease to severe, lifelong, transfusion-dependent anemia with multiorgan involvement. Stem-cell transplantation is the preferred treatment for severe forms of thalassemia. Supportive, rather than curative, treatment consists of periodic blood transfusions for life combined with iron chelation. Drugs to treat the symptoms of sickle-cell disease include analgesics, antibiotics, ACE inhibitors, and hydroxyurea. Blood transfusions should be given only when strictly indicated. More than 90% of patients currently survive into adulthood. Optimally treated patients have a projected life span of 50 to 60 years. With approximately 7% of the worldwide population being carriers, hemoglobinopathies are the most common monogenic diseases and one of the world’s major health problems. They were originally found mainly in the Mediterranean area and large parts of Asia and Africa. International migration has spread them from those areas all over the world. In many parts of Europe today, hemoglobin (Hb) defects are classified as endemic diseases.

Market Dynamics

Increasing launches of new products and mergers and acquisitions by key market players are expected to drive the global hemoglobinopathy treatment drugs market growth. For instance, on August 8, 2022, Pfizer Inc., a U.S.-based multinational pharmaceutical and biotechnology corporation, and Global Blood Therapeutics, Inc., a U.S.-based Healthcare company, announced that the companies have entered into a definitive agreement under which Pfizer will acquire GBT. Under the terms of the transaction, Pfizer Inc will acquire all the outstanding shares of Global Blood Therapeutics, Inc. for US$ 68.50 per share in cash, for a total enterprise value of approximately US$ 5.4 billion, including debt and net of cash acquired. The Boards of Directors of both companies have unanimously approved the transaction.

Key features of the study:
  • This report provides an in-depth analysis of the global hemoglobinopathy treatment drugs market and provides market size (US$ Billion) and compound annual growth rate (CAGR) for the forecast period (2023–2030), considering 2022 as the base year
  • It elucidates potential revenue opportunities across different segments and explains attractive investment proposition matrices for this market
  • This study also provides key insights about market drivers, restraints, opportunities, new product launches or approval, market trends, regional outlook, and competitive strategies adopted by key players
  • It profiles key players in the global hemoglobinopathy treatment drugs market based on the following parameters– company highlights, products portfolio, key highlights, financial performance, and strategies
  • Key companies covered as a part of this study include Bristol-Myers Squibb Company, GlycoMimetics Inc., Pfizer Inc., Anthera Pharmaceuticals Inc., Eli Lilly and Company, Mast Therapeutics, Daiichi Sankyo Company Ltd., Novartis International AG, Bluebird Bio Inc., HemaQuest Pharmaceuticals Inc., Emmaus Medical Inc., Baxter International Inc., Prolong Pharmaceuticals, Medunik USA Inc., Sangamo Therapeutics, Inc., Global Blood Therapeutics, Alnylam Pharmaceuticals, and Acceleron Pharma, Inc.
  • Global hemoglobinopathy treatment drugs market report caters to various stakeholders in this industry including investors, suppliers, product manufacturers, distributors, new entrants, and financial analysts
  • Stakeholders would have ease in decision-making through various strategy matrices used in analyzing the global hemoglobinopathy treatment drugs market
Detailed Segmentation:
  • Global Hemoglobinopathy Treatment Drugs Market, By Drug Type:
  • Analgesics
  • Antibiotics
  • ACE Inhibitors
  • Hydroxyurea
  • Others
  • Global Hemoglobinopathy Treatment Drugs Market, By Disease Type:
  • Thalassemia
  • Sickle Cell Disease
  • Other Hb Variants Diseases
  • Global Hemoglobinopathy Treatment Drugs Market, By Distribution Channel:
  • Hospitals Pharmacies
  • Retail Pharmacies
  • Online Pharmacies
  • Global Hemoglobinopathy Treatment Drugs Market, By Region:
  • North America
  • U.S.
  • Canada
  • Europe
  • U.K.
  • Germany
  • Italy
  • Spain
  • France
  • Russia
  • Rest of Europe
  • Asia Pacific
  • Australia
  • India
  • China
  • Japan
  • ASEAN
  • South Korea
  • Rest of Asia Pacific
  • Latin America
  • Brazil
  • Mexico
  • Argentina
  • Middle East
  • GCC Countries
  • Israel
  • Rest of Middle East
  • Africa
  • South Africa
  • Central Africa
  • North Africa
  • Company Profiles
  • Bristol-Myers Squibb Company
  • GlycoMimetics Inc.
  • Pfizer Inc.
  • Anthera Pharmaceuticals Inc.
  • Eli Lilly and Company
  • Mast Therapeutics
  • Daiichi Sankyo Company Ltd.
  • Novartis International AG
  • Bluebird Bio Inc.
  • HemaQuest Pharmaceuticals Inc.
  • Emmaus Medical Inc.
  • Baxter International Inc.
  • Prolong Pharmaceuticals
  • Medunik USA Inc.
  • Sangamo Therapeutics, Inc.
  • Global Blood Therapeutics, Inc.
  • Alnylam Pharmaceuticals
  • Acceleron Pharma, Inc.


1. Research Objectives and Assumptions
Research Objectives
Assumptions
Abbreviations
2. Market Purview
Report Description
Market Definition and Scope
Executive Summary
Market Snapshot, By Drug Type
Market Snapshot, By Disease Type
Market Snapshot, By Distribution Channel
Market Snapshot, By Region
Coherent Opportunity Map (COM)
3. Market Dynamics, Regulations, and Trends Analysis
Market Dynamics
Drivers
Restraints
Market Opportunities
Impact Analysis
Recent Product Launches
Epidemiology
Merger, Acquisition, and Collaborations
Regulatory Scenario
Key Developments
PEST Analysis
4. Global Hemoglobinopathy Treatment Drugs Market– COVID-19 Impact Analysis
Economic Impact
COVID-19 Epidemiology
Impact on Supply and Demand
5. Global Hemoglobinopathy Treatment Drugs Market, By Drug Type, 2018–2030, (US$ Billion)
Introduction
Market Share Analysis, 2023 and 2030 (%)
Y-o-Y Growth Analysis, 2018–2030
Segment Trends
Analgesics
Introduction
Market Size and Forecast, and Y-o-Y Growth, 2018–2030, (US$ Billion)
Antibiotics
Introduction
Market Size and Forecast, and Y-o-Y Growth, 2018–2030, (US$ Billion)
ACE Inhibitors
Introduction
Market Size and Forecast, and Y-o-Y Growth, 2018–2030, (US$ Billion)
Hydroxyurea
Introduction
Market Size and Forecast, and Y-o-Y Growth, 2018–2030, (US$ Billion)
Others
Introduction
Market Size and Forecast, and Y-o-Y Growth, 2018–2030, (US$ Billion)
6. Global Hemoglobinopathy Treatment Drugs Market, By Disease Type, 2018–2030, (US$ Billion)
Introduction
Market Share Analysis, 2023 and 2030 (%)
Y-o-Y Growth Analysis, 2018–2030
Segment Trends
Thalassemia
Introduction
Market Size and Forecast, and Y-o-Y Growth, 2018–2030, (US$ Billion)
Sickle Cell Disease
Introduction
Market Size and Forecast, and Y-o-Y Growth, 2018–2030, (US$ Billion)
Other Hb Variants Diseases
Introduction
Market Size and Forecast, and Y-o-Y Growth, 2018–2030, (US$ Billion)
7. Global Hemoglobinopathy Treatment Drugs Market, By Distribution Channel, 2018–2030, (US$ Billion)
Introduction
Market Share Analysis, 2023 and 2030 (%)
Y-o-Y Growth Analysis, 2018–2030
Segment Trends
Hospitals Pharmacies
Introduction
Market Size and Forecast, and Y-o-Y Growth, 2018–2030, (US$ Billion)
Retail Pharmacies
Introduction
Market Size and Forecast, and Y-o-Y Growth, 2018–2030, (US$ Billion)
Online Pharmacies
Introduction
Market Size and Forecast, and Y-o-Y Growth, 2018–2030, (US$ Billion)
8. Global Hemoglobinopathy Treatment Drugs Market, By Region, 2018–2030, (US$ Billion)
Introduction
Market Share Analysis, By Region, 2023 and 2030 (%)
Y-o-Y Growth Analysis, For Region, 2018–2030
Regional Trends
North America
Introduction
Market Size and Forecast, and Y-o-Y Growth, By Drug type, 2018 - 2030, (US$ Billion)
Market Size and Forecast, and Y-o-Y Growth, By Disease Type, 2018 - 2030, (US$ Billion)
Market Size and Forecast, and Y-o-Y Growth, By Distribution Channel, 2018 - 2030, (US$ Billion)
Market Size and Forecast, and Y-o-Y Growth, By Country, 2018–2030, (US$ Billion)
U.S.
Canada
Latin America
Introduction
Market Size and Forecast, and Y-o-Y Growth, By Drug type, 2018 - 2030, (US$ Billion)
Market Size and Forecast, and Y-o-Y Growth, By Disease Type, 2018 - 2030, (US$ Billion)
Market Size and Forecast, and Y-o-Y Growth, By Distribution Channel, 2018 - 2030, (US$ Billion)
Market Size and Forecast, and Y-o-Y Growth, By Country, 2018–2030, (US$ Billion)
Brazil
Mexico
Argentina
Rest of Latin America
Europe
Introduction
Market Size and Forecast, and Y-o-Y Growth, By Drug type, 2018 - 2030, (US$ Billion)
Market Size and Forecast, and Y-o-Y Growth, By Disease Type, 2018 - 2030, (US$ Billion)
Market Size and Forecast, and Y-o-Y Growth, By Distribution Channel, 2018 - 2030, (US$ Billion)
Market Size and Forecast, and Y-o-Y Growth, By Country, 2018–2030, (US$ Billion)
U.K.
Germany
Italy
France
Spain
Russia
Rest of Europe
Asia Pacific
Introduction
Market Size and Forecast, and Y-o-Y Growth, By Drug type, 2018 - 2030, (US$ Billion)
Market Size and Forecast, and Y-o-Y Growth, By Disease Type, 2018 - 2030, (US$ Billion)
Market Size and Forecast, and Y-o-Y Growth, By Distribution Channel, 2018 - 2030, (US$ Billion)
Market Size and Forecast, and Y-o-Y Growth, By Country, 2018–2030, (US$ Billion)
China
India
Japan
ASEAN
Australia
South Korea
Rest of Asia Pacific
Middle East
Introduction
Market Size and Forecast, and Y-o-Y Growth, By Drug type, 2018 - 2030, (US$ Billion)
Market Size and Forecast, and Y-o-Y Growth, By Disease Type, 2018 - 2030, (US$ Billion)
Market Size and Forecast, and Y-o-Y Growth, By Distribution Channel, 2018 - 2030, (US$ Billion)
Market Size and Forecast, and Y-o-Y Growth, By Country, 2018–2030, (US$ Billion)
GCC
Israel
Rest of Middle East
Africa
Introduction
Market Size and Forecast, and Y-o-Y Growth, By Drug type, 2018 - 2030, (US$ Billion)
Market Size and Forecast, and Y-o-Y Growth, By Disease Type, 2018 - 2030, (US$ Billion)
Market Size and Forecast, and Y-o-Y Growth, By Distribution Channel, 2018 - 2030, (US$ Billion)
Market Size and Forecast, and Y-o-Y Growth, By Country/Sub-region, 2018–2030, (US$ Billion)
North Africa
Central Africa
South Africa
9. Competitive Landscape
Bristol-Myers Squibb Company
Company Highlights
Product Portfolio
Key Highlights
Financial Performance
Market Strategies
GlycoMimetics Inc.
Company Highlights
Product Portfolio
Key Highlights
Financial Performance
Market Strategies
Pfizer Inc.
Company Highlights
Product Portfolio
Key Highlights
Financial Performance
Market Strategies
Anthera Pharmaceuticals Inc.
Company Highlights
Product Portfolio
Key Highlights
Financial Performance
Market Strategies
Eli Lilly and Company
Company Highlights
Product Portfolio
Key Highlights
Financial Performance
Market Strategies
Mast Therapeutics
Company Highlights
Product Portfolio
Key Highlights
Financial Performance
Market Strategies
Daiichi Sankyo Company Ltd.
Company Highlights
Product Portfolio
Key Highlights
Financial Performance
Market Strategies
Novartis International AG
Company Highlights
Product Portfolio
Key Highlights
Financial Performance
Market Strategies
Bluebird Bio Inc.
Company Highlights
Product Portfolio
Key Highlights
Financial Performance
Market Strategies
HemaQuest Pharmaceuticals Inc.
Company Highlights
Product Portfolio
Key Highlights
Financial Performance
Market Strategies
Emmaus Medical Inc.
Company Highlights
Product Portfolio
Key Highlights
Financial Performance
Market Strategies
Baxter International Inc.
Company Highlights
Product Portfolio
Key Highlights
Financial Performance
Prolong Pharmaceuticals
Company Highlights
Product Portfolio
Key Highlights
Financial Performance
Medunik USA Inc.
Company Highlights
Product Portfolio
Key Highlights
Financial Performance
Sangamo Therapeutics, Inc.
Company Highlights
Product Portfolio
Key Highlights
Financial Performance
Global Blood Therapeutics
Company Highlights
Product Portfolio
Key Highlights
Financial Performance
Alnylam Pharmaceuticals
Company Highlights
Product Portfolio
Key Highlights
Financial Performance
Market Strategies
Acceleron Pharma, Inc.
Company Highlights
Product Portfolio
Key Highlights
Financial Performance
Market Strategies
10. Section
Research Methodology
About Us
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