Rare Diseases Treatment Global Market Report 2025 from The Business Research Company provides strategists, marketers and senior management with the critical information they need to assess the market.
This report focuses on rare diseases treatment market which is experiencing strong growth. The report gives a guide to the trends which will be shaping the market over the next ten years and beyond.
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Where is the largest and fastest growing market for rare diseases treatment ? How does the market relate to the overall economy, demography and other similar markets? What forces will shape the market going forward? The rare diseases treatment market global report from the Business Research Company answers all these questions and many more.
The report covers market characteristics, size and growth, segmentation, regional and country breakdowns, competitive landscape, market shares, trends and strategies for this market. It traces the market’s historic and forecast market growth by geography.
- The market characteristics section of the report defines and explains the market.
- The market size section gives the market size ($b) covering both the historic growth of the market, and forecasting its development.
- The forecasts are made after considering the major factors currently impacting the market. These include:
- The forecasts are made after considering the major factors currently impacting the market. These include the Russia-Ukraine war, rising inflation, higher interest rates, and the legacy of the COVID-19 pandemic.
- Market segmentations break down the market into sub markets.
- The regional and country breakdowns section gives an analysis of the market in each geography and the size of the market by geography and compares their historic and forecast growth. It covers the growth trajectory of COVID-19 for all regions, key developed countries and major emerging markets.
- The competitive landscape chapter gives a description of the competitive nature of the market, market shares, and a description of the leading companies. Key financial deals which have shaped the market in recent years are identified.
- The trends and strategies section analyses the shape of the market as it emerges from the crisis and suggests how companies can grow as the market recovers.
Markets Covered:1) By Drug Type: Originator Drugs (Patented Molecules); Generic Drugs
2) By Drug Class: Biologics; Organic Compounds
3) By Mode Of Administration: Injectable; Oral; Other Modes Of Administration
4) By Therapeutic Area: Cancer; Neurological Conditions; Cardiovascular Conditions; Musculoskeletal Conditions; Hematologic Disorders; Infectious Diseases; Metabolic Disorders; Endocrine Disorders; Other Therapeutic Areas
5) By Distribution Channel: Hospital Pharmacies; Specialty Pharmacies; Retail Pharmacies
Subsegments:
1) By Originator Drugs: Monoclonal Antibodies; Enzyme Replacement Therapies; Gene Therapies; Small Molecule Drugs
2) By Generic Drugs: Generic Monoclonal Antibodies; Generic Enzyme Replacement Therapies; Generic Small Molecule Drugs; Biosimilars
Companies Mentioned: AbbVie Inc.; Actelion Pharmaceuticals Ltd; Alexion Pharmaceuticals Inc.; Celgene Corporation; Bayer AG
Countries: Australia; Brazil; China; France; Germany; India; Indonesia; Japan; Russia; South Korea; UK; USA; Canada; Italy; Spain
Regions: Asia-Pacific; Western Europe; Eastern Europe; North America; South America; Middle East; Africa
Time series: Five years historic and ten years forecast.
Data: Ratios of market size and growth to related markets, GDP proportions, expenditure per capita,
Data segmentations: country and regional historic and forecast data, market share of competitors, market segments.
Sourcing and Referencing: Data and analysis throughout the report is sourced using end notes.
Delivery format: PDF, Word and Excel Data Dashboard.
Please Note: Report will be updated with the latest data and delivered to you within 3-5 working days of order.
- 1. Executive Summary
- 2. Rare Diseases Treatment Market Characteristics
- 3. Rare Diseases Treatment Market Trends And Strategies
- 4. Rare Diseases Treatment Market - Macro Economic Scenario Including The Impact Of Interest Rates, Inflation, Geopolitics And Covid And Recovery On The Market
- 5. Global Rare Diseases Treatment Growth Analysis And Strategic Analysis Framework
- 5.1. Global Rare Diseases Treatment PESTEL Analysis (Political, Social, Technological, Environmental and Legal Factors, Drivers and Restraints)
- 5.2. Analysis Of End Use Industries
- 5.3. Global Rare Diseases Treatment Market Growth Rate Analysis
- 5.4. Global Rare Diseases Treatment Historic Market Size and Growth, 2019 - 2024, Value ($ Billion)
- 5.5. Global Rare Diseases Treatment Forecast Market Size and Growth, 2024 - 2029, 2034F, Value ($ Billion)
- 5.6. Global Rare Diseases Treatment Total Addressable Market (TAM)
- 6. Rare Diseases Treatment Market Segmentation
- 6.1. Global Rare Diseases Treatment Market, Segmentation By Drug Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
- Originator Drugs (Patented Molecules)
- Generic Drugs
- 6.2. Global Rare Diseases Treatment Market, Segmentation By Drug Class, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
- Biologics
- Organic Compounds
- 6.3. Global Rare Diseases Treatment Market, Segmentation By Mode Of Administration, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
- Injectable
- Oral
- Other Modes Of Administration
- 6.4. Global Rare Diseases Treatment Market, Segmentation By Therapeutic Area, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
- Cancer
- Neurological Conditions
- Cardiovascular Conditions
- Musculoskeletal Conditions
- Hematologic Disorders
- Infectious Diseases
- Metabolic Disorders
- Endocrine Disorders
- Other Therapeutic Areas
- 6.5. Global Rare Diseases Treatment Market, Segmentation By Distribution Channel, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
- Hospital Pharmacies
- Specialty Pharmacies
- Retail Pharmacies
- 6.6. Global Rare Diseases Treatment Market, Sub-Segmentation Of Originator Drugs, By Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
- Monoclonal Antibodies
- Enzyme Replacement Therapies
- Gene Therapies
- Small Molecule Drugs
- 6.7. Global Rare Diseases Treatment Market, Sub-Segmentation Of Generic Drugs, By Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
- Generic Monoclonal Antibodies
- Generic Enzyme Replacement Therapies
- Generic Small Molecule Drugs
- Biosimilars
- 7. Rare Diseases Treatment Market Regional And Country Analysis
- 7.1. Global Rare Diseases Treatment Market, Split By Region, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
- 7.2. Global Rare Diseases Treatment Market, Split By Country, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
- 8. Asia-Pacific Rare Diseases Treatment Market
- 8.1. Asia-Pacific Rare Diseases Treatment Market Overview
- Region Information, Market Information, Background Information, Government Initiatives, Regulations, Regulatory Bodies, Major Associations, Taxes Levied, Corporate Tax Structure, Investments, Major Companies
- 8.2. Asia-Pacific Rare Diseases Treatment Market, Segmentation By Drug Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
- 8.3. Asia-Pacific Rare Diseases Treatment Market, Segmentation By Drug Class, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
- 8.4. Asia-Pacific Rare Diseases Treatment Market, Segmentation By Mode Of Administration, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
- 9. China Rare Diseases Treatment Market
- 9.1. China Rare Diseases Treatment Market Overview
- 9.2. China Rare Diseases Treatment Market, Segmentation By Drug Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F,$ Billion
- 9.3. China Rare Diseases Treatment Market, Segmentation By Drug Class, Historic and Forecast, 2019-2024, 2024-2029F, 2034F,$ Billion
- 9.4. China Rare Diseases Treatment Market, Segmentation By Mode Of Administration, Historic and Forecast, 2019-2024, 2024-2029F, 2034F,$ Billion
- 10. India Rare Diseases Treatment Market
- 10.1. India Rare Diseases Treatment Market, Segmentation By Drug Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
- 10.2. India Rare Diseases Treatment Market, Segmentation By Drug Class, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
- 10.3. India Rare Diseases Treatment Market, Segmentation By Mode Of Administration, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
- 11. Japan Rare Diseases Treatment Market
- 11.1. Japan Rare Diseases Treatment Market Overview
- 11.2. Japan Rare Diseases Treatment Market, Segmentation By Drug Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
- 11.3. Japan Rare Diseases Treatment Market, Segmentation By Drug Class, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
- 11.4. Japan Rare Diseases Treatment Market, Segmentation By Mode Of Administration, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
- 12. Australia Rare Diseases Treatment Market
- 12.1. Australia Rare Diseases Treatment Market, Segmentation By Drug Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
- 12.2. Australia Rare Diseases Treatment Market, Segmentation By Drug Class, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
- 12.3. Australia Rare Diseases Treatment Market, Segmentation By Mode Of Administration, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
- 13. Indonesia Rare Diseases Treatment Market
- 13.1. Indonesia Rare Diseases Treatment Market, Segmentation By Drug Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
- 13.2. Indonesia Rare Diseases Treatment Market, Segmentation By Drug Class, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
- 13.3. Indonesia Rare Diseases Treatment Market, Segmentation By Mode Of Administration, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
- 14. South Korea Rare Diseases Treatment Market
- 14.1. South Korea Rare Diseases Treatment Market Overview
- 14.2. South Korea Rare Diseases Treatment Market, Segmentation By Drug Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
- 14.3. South Korea Rare Diseases Treatment Market, Segmentation By Drug Class, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
- 14.4. South Korea Rare Diseases Treatment Market, Segmentation By Mode Of Administration, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
- 15. Western Europe Rare Diseases Treatment Market
- 15.1. Western Europe Rare Diseases Treatment Market Overview
- 15.2. Western Europe Rare Diseases Treatment Market, Segmentation By Drug Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
- 15.3. Western Europe Rare Diseases Treatment Market, Segmentation By Drug Class, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
- 15.4. Western Europe Rare Diseases Treatment Market, Segmentation By Mode Of Administration, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
- 16. UK Rare Diseases Treatment Market
- 16.1. UK Rare Diseases Treatment Market, Segmentation By Drug Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
- 16.2. UK Rare Diseases Treatment Market, Segmentation By Drug Class, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
- 16.3. UK Rare Diseases Treatment Market, Segmentation By Mode Of Administration, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
- 17. Germany Rare Diseases Treatment Market
- 17.1. Germany Rare Diseases Treatment Market, Segmentation By Drug Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
- 17.2. Germany Rare Diseases Treatment Market, Segmentation By Drug Class, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
- 17.3. Germany Rare Diseases Treatment Market, Segmentation By Mode Of Administration, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
- 18. France Rare Diseases Treatment Market
- 18.1. France Rare Diseases Treatment Market, Segmentation By Drug Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
- 18.2. France Rare Diseases Treatment Market, Segmentation By Drug Class, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
- 18.3. France Rare Diseases Treatment Market, Segmentation By Mode Of Administration, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
- 19. Italy Rare Diseases Treatment Market
- 19.1. Italy Rare Diseases Treatment Market, Segmentation By Drug Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
- 19.2. Italy Rare Diseases Treatment Market, Segmentation By Drug Class, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
- 19.3. Italy Rare Diseases Treatment Market, Segmentation By Mode Of Administration, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
- 20. Spain Rare Diseases Treatment Market
- 20.1. Spain Rare Diseases Treatment Market, Segmentation By Drug Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
- 20.2. Spain Rare Diseases Treatment Market, Segmentation By Drug Class, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
- 20.3. Spain Rare Diseases Treatment Market, Segmentation By Mode Of Administration, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
- 21. Eastern Europe Rare Diseases Treatment Market
- 21.1. Eastern Europe Rare Diseases Treatment Market Overview
- 21.2. Eastern Europe Rare Diseases Treatment Market, Segmentation By Drug Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
- 21.3. Eastern Europe Rare Diseases Treatment Market, Segmentation By Drug Class, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
- 21.4. Eastern Europe Rare Diseases Treatment Market, Segmentation By Mode Of Administration, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
- 22. Russia Rare Diseases Treatment Market
- 22.1. Russia Rare Diseases Treatment Market, Segmentation By Drug Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
- 22.2. Russia Rare Diseases Treatment Market, Segmentation By Drug Class, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
- 22.3. Russia Rare Diseases Treatment Market, Segmentation By Mode Of Administration, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
- 23. North America Rare Diseases Treatment Market
- 23.1. North America Rare Diseases Treatment Market Overview
- 23.2. North America Rare Diseases Treatment Market, Segmentation By Drug Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
- 23.3. North America Rare Diseases Treatment Market, Segmentation By Drug Class, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
- 23.4. North America Rare Diseases Treatment Market, Segmentation By Mode Of Administration, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
- 24. USA Rare Diseases Treatment Market
- 24.1. USA Rare Diseases Treatment Market Overview
- 24.2. USA Rare Diseases Treatment Market, Segmentation By Drug Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
- 24.3. USA Rare Diseases Treatment Market, Segmentation By Drug Class, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
- 24.4. USA Rare Diseases Treatment Market, Segmentation By Mode Of Administration, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
- 25. Canada Rare Diseases Treatment Market
- 25.1. Canada Rare Diseases Treatment Market Overview
- 25.2. Canada Rare Diseases Treatment Market, Segmentation By Drug Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
- 25.3. Canada Rare Diseases Treatment Market, Segmentation By Drug Class, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
- 25.4. Canada Rare Diseases Treatment Market, Segmentation By Mode Of Administration, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
- 26. South America Rare Diseases Treatment Market
- 26.1. South America Rare Diseases Treatment Market Overview
- 26.2. South America Rare Diseases Treatment Market, Segmentation By Drug Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
- 26.3. South America Rare Diseases Treatment Market, Segmentation By Drug Class, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
- 26.4. South America Rare Diseases Treatment Market, Segmentation By Mode Of Administration, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
- 27. Brazil Rare Diseases Treatment Market
- 27.1. Brazil Rare Diseases Treatment Market, Segmentation By Drug Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
- 27.2. Brazil Rare Diseases Treatment Market, Segmentation By Drug Class, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
- 27.3. Brazil Rare Diseases Treatment Market, Segmentation By Mode Of Administration, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
- 28. Middle East Rare Diseases Treatment Market
- 28.1. Middle East Rare Diseases Treatment Market Overview
- 28.2. Middle East Rare Diseases Treatment Market, Segmentation By Drug Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
- 28.3. Middle East Rare Diseases Treatment Market, Segmentation By Drug Class, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
- 28.4. Middle East Rare Diseases Treatment Market, Segmentation By Mode Of Administration, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
- 29. Africa Rare Diseases Treatment Market
- 29.1. Africa Rare Diseases Treatment Market Overview
- 29.2. Africa Rare Diseases Treatment Market, Segmentation By Drug Type, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
- 29.3. Africa Rare Diseases Treatment Market, Segmentation By Drug Class, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
- 29.4. Africa Rare Diseases Treatment Market, Segmentation By Mode Of Administration, Historic and Forecast, 2019-2024, 2024-2029F, 2034F, $ Billion
- 30. Rare Diseases Treatment Market Competitive Landscape And Company Profiles
- 30.1. Rare Diseases Treatment Market Competitive Landscape
- 30.2. Rare Diseases Treatment Market Company Profiles
- 30.2.1. AbbVie Inc. Overview, Products and Services, Strategy and Financial Analysis
- 30.2.2. Actelion Pharmaceuticals Ltd. Overview, Products and Services, Strategy and Financial Analysis
- 30.2.3. Alexion Pharmaceuticals Inc. Overview, Products and Services, Strategy and Financial Analysis
- 30.2.4. Celgene Corporation Overview, Products and Services, Strategy and Financial Analysis
- 30.2.5. Bayer AG Overview, Products and Services, Strategy and Financial Analysis
- 31. Rare Diseases Treatment Market Other Major And Innovative Companies
- 31.1. Johnson & Johnson
- 31.2. Novartis AG
- 31.3. Pfizer Inc.
- 31.4. Sanofi S.A.
- 31.5. Eisai Co. Ltd.
- 31.6. Merck & Co. Inc.
- 31.7. Vertex Pharmaceuticals
- 31.8. Takeda Pharmaceutical Company
- 31.9. Eli Lilly and Company
- 31.10. AstraZeneca PLC
- 31.11. Abeona Therapeutics Inc.
- 31.12. Akcea Therapeutics Inc.
- 31.13. Alnylam Pharmaceuticals Inc.
- 31.14. Amicus Therapeutics Inc.
- 31.15. BioMarin Pharmaceutical Inc.
- 32. Global Rare Diseases Treatment Market Competitive Benchmarking And Dashboard
- 33. Key Mergers And Acquisitions In The Rare Diseases Treatment Market
- 34. Recent Developments In The Rare Diseases Treatment Market
- 35. Rare Diseases Treatment Market High Potential Countries, Segments and Strategies
- 35.1 Rare Diseases Treatment Market In 2029 - Countries Offering Most New Opportunities
- 35.2 Rare Diseases Treatment Market In 2029 - Segments Offering Most New Opportunities
- 35.3 Rare Diseases Treatment Market In 2029 - Growth Strategies
- 35.3.1 Market Trend Based Strategies
- 35.3.2 Competitor Strategies
- 36. Appendix
- 36.1. Abbreviations
- 36.2. Currencies
- 36.3. Historic And Forecast Inflation Rates
- 36.4. Research Inquiries
- 36.5. The Business Research Company
- 36.6. Copyright And Disclaimer
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