Orphan Drugs Market by Disease Type (Gastrointestinal, Hematology, Infectious Diseases), Product Type (Biologic, Non-Biologic), Distribution Channel - Global Forecast 2024-2030

Orphan Drugs Market by Disease Type (Gastrointestinal, Hematology, Infectious Diseases), Product Type (Biologic, Non-Biologic), Distribution Channel - Global Forecast 2024-2030


The Orphan Drugs Market size was estimated at USD 191.86 billion in 2023 and expected to reach USD 216.80 billion in 2024, at a CAGR 13.39% to reach USD 462.45 billion by 2030.

Global Orphan Drugs Market

FPNV Positioning Matrix

The FPNV Positioning Matrix is pivotal in evaluating the Orphan Drugs Market. It offers a comprehensive assessment of vendors, examining key metrics related to Business Strategy and Product Satisfaction. This in-depth analysis empowers users to make well-informed decisions aligned with their requirements. Based on the evaluation, the vendors are then categorized into four distinct quadrants representing varying levels of success: Forefront (F), Pathfinder (P), Niche (N), or Vital (V).

Market Share Analysis

The Market Share Analysis is a comprehensive tool that provides an insightful and in-depth examination of the current state of vendors in the Orphan Drugs Market. By meticulously comparing and analyzing vendor contributions in terms of overall revenue, customer base, and other key metrics, we can offer companies a greater understanding of their performance and the challenges they face when competing for market share. Additionally, this analysis provides valuable insights into the competitive nature of the sector, including factors such as accumulation, fragmentation dominance, and amalgamation traits observed over the base year period studied. With this expanded level of detail, vendors can make more informed decisions and devise effective strategies to gain a competitive edge in the market.

Key Company Profiles

The report delves into recent significant developments in the Orphan Drugs Market, highlighting leading vendors and their innovative profiles. These include Alexion Pharmaceuticals, Inc., AstraZeneca PLC, Bayer AG, Belite Bio Inc, Biogen Inc., Dynacure SA, Eisai Co. Ltd., Eli Lilly and Company, F. Hoffmann-La Roche Ltd, GlaxoSmithKline PLC, Johnson & Johnson Services, Inc., MeiraGTx Limited, Novartis AG, Pfizer Inc., and Sanofi S.A..

Market Segmentation & Coverage

This research report categorizes the Orphan Drugs Market to forecast the revenues and analyze trends in each of the following sub-markets:

Disease Type
Gastrointestinal
Hematology
Infectious Diseases
Neurology
Oncology
Pulmonary
Product Type
Biologic
Non-Biologic
Distribution Channel
Hospital Pharmacies
Retail Pharmacies
Specialty Pharmacies
Region
Americas
Argentina
Brazil
Canada
Mexico
United States
California
Florida
Illinois
New York
Ohio
Pennsylvania
Texas
Asia-Pacific
Australia
China
India
Indonesia
Japan
Malaysia
Philippines
Singapore
South Korea
Taiwan
Thailand
Vietnam
Europe, Middle East & Africa
Denmark
Egypt
Finland
France
Germany
Israel
Italy
Netherlands
Nigeria
Norway
Poland
Qatar
Russia
Saudi Arabia
South Africa
Spain
Sweden
Switzerland
Turkey
United Arab Emirates
United Kingdom

The report offers valuable insights on the following aspects:

1. Market Penetration: It presents comprehensive information on the market provided by key players.
2. Market Development: It delves deep into lucrative emerging markets and analyzes the penetration across mature market segments.
3. Market Diversification: It provides detailed information on new product launches, untapped geographic regions, recent developments, and investments.
4. Competitive Assessment & Intelligence: It conducts an exhaustive assessment of market shares, strategies, products, certifications, regulatory approvals, patent landscape, and manufacturing capabilities of the leading players.
5. Product Development & Innovation: It offers intelligent insights on future technologies, R&D activities, and breakthrough product developments.

The report addresses key questions such as:

1. What is the market size and forecast of the Orphan Drugs Market?
2. Which products, segments, applications, and areas should one consider investing in over the forecast period in the Orphan Drugs Market?
3. What are the technology trends and regulatory frameworks in the Orphan Drugs Market?
4. What is the market share of the leading vendors in the Orphan Drugs Market?
5. Which modes and strategic moves are suitable for entering the Orphan Drugs Market?

Note: PDF & Excel + Online Access - 1 Year


1. Preface
1.1. Objectives of the Study
1.2. Market Segmentation & Coverage
1.3. Years Considered for the Study
1.4. Currency & Pricing
1.5. Language
1.6. Limitations
1.7. Assumptions
1.8. Stakeholders
2. Research Methodology
2.1. Define: Research Objective
2.2. Determine: Research Design
2.3. Prepare: Research Instrument
2.4. Collect: Data Source
2.5. Analyze: Data Interpretation
2.6. Formulate: Data Verification
2.7. Publish: Research Report
2.8. Repeat: Report Update
3. Executive Summary
4. Market Overview
4.1. Introduction
4.2. Orphan Drugs Market, by Region
5. Market Insights
5.1. Market Dynamics
5.1.1. Drivers
5.1.1.1. Surge in prevalence of rare diseases and increasing healthcare expenditure
5.1.1.2. Favorable government and economic incentives for the development of drugs for rare diseases
5.1.1.3. Availability of exclusivity for orphan drugs
5.1.2. Restraints
5.1.2.1. High cost associated with orphan drugs
5.1.3. Opportunities
5.1.3.1. Increasing R&D initiatives and development of novel products
5.1.3.2. Regulatory incentives for the development of orphan drugs in emerging countries
5.1.4. Challenges
5.1.4.1. Side effects associated with orphan drugs
5.2. Market Segmentation Analysis
5.3. Market Trend Analysis
5.4. Cumulative Impact of High Inflation
5.5. Porter’s Five Forces Analysis
5.5.1. Threat of New Entrants
5.5.2. Threat of Substitutes
5.5.3. Bargaining Power of Customers
5.5.4. Bargaining Power of Suppliers
5.5.5. Industry Rivalry
5.6. Value Chain & Critical Path Analysis
5.7. Regulatory Framework
6. Orphan Drugs Market, by Disease Type
6.1. Introduction
6.2. Gastrointestinal
6.3. Hematology
6.4. Infectious Diseases
6.5. Neurology
6.6. Oncology
6.7. Pulmonary
7. Orphan Drugs Market, by Product Type
7.1. Introduction
7.2. Biologic
7.3. Non-Biologic
8. Orphan Drugs Market, by Distribution Channel
8.1. Introduction
8.2. Hospital Pharmacies
8.3. Retail Pharmacies
8.4. Specialty Pharmacies
9. Americas Orphan Drugs Market
9.1. Introduction
9.2. Argentina
9.3. Brazil
9.4. Canada
9.5. Mexico
9.6. United States
10. Asia-Pacific Orphan Drugs Market
10.1. Introduction
10.2. Australia
10.3. China
10.4. India
10.5. Indonesia
10.6. Japan
10.7. Malaysia
10.8. Philippines
10.9. Singapore
10.10. South Korea
10.11. Taiwan
10.12. Thailand
10.13. Vietnam
11. Europe, Middle East & Africa Orphan Drugs Market
11.1. Introduction
11.2. Denmark
11.3. Egypt
11.4. Finland
11.5. France
11.6. Germany
11.7. Israel
11.8. Italy
11.9. Netherlands
11.10. Nigeria
11.11. Norway
11.12. Poland
11.13. Qatar
11.14. Russia
11.15. Saudi Arabia
11.16. South Africa
11.17. Spain
11.18. Sweden
11.19. Switzerland
11.20. Turkey
11.21. United Arab Emirates
11.22. United Kingdom
12. Competitive Landscape
12.1. FPNV Positioning Matrix
12.2. Market Share Analysis, By Key Player
12.3. Competitive Scenario Analysis, By Key Player
13. Competitive Portfolio
13.1. Key Company Profiles
13.1.1. Alexion Pharmaceuticals, Inc.
13.1.2. AstraZeneca PLC
13.1.3. Bayer AG
13.1.4. Belite Bio Inc
13.1.5. Biogen Inc.
13.1.6. Dynacure SA
13.1.7. Eisai Co. Ltd.
13.1.8. Eli Lilly and Company
13.1.9. F. Hoffmann-La Roche Ltd
13.1.10. GlaxoSmithKline PLC
13.1.11. Johnson & Johnson Services, Inc.
13.1.12. MeiraGTx Limited
13.1.13. Novartis AG
13.1.14. Pfizer Inc.
13.1.15. Sanofi S.A.
13.2. Key Product Portfolio
14. Appendix
14.1. Discussion Guide
14.2. License & Pricing
FIGURE 1. ORPHAN DRUGS MARKET RESEARCH PROCESS
FIGURE 2. ORPHAN DRUGS MARKET SIZE, 2023 VS 2030
FIGURE 3. ORPHAN DRUGS MARKET SIZE, 2018-2030 (USD MILLION)
FIGURE 4. ORPHAN DRUGS MARKET SIZE, BY REGION, 2023 VS 2030 (%)
FIGURE 5. ORPHAN DRUGS MARKET SIZE, BY REGION, 2023 VS 2024 VS 2030 (USD MILLION)
FIGURE 6. ORPHAN DRUGS MARKET DYNAMICS
FIGURE 7. ORPHAN DRUGS MARKET SIZE, BY DISEASE TYPE, 2023 VS 2030 (%)
FIGURE 8. ORPHAN DRUGS MARKET SIZE, BY DISEASE TYPE, 2023 VS 2024 VS 2030 (USD MILLION)
FIGURE 9. ORPHAN DRUGS MARKET SIZE, BY PRODUCT TYPE, 2023 VS 2030 (%)
FIGURE 10. ORPHAN DRUGS MARKET SIZE, BY PRODUCT TYPE, 2023 VS 2024 VS 2030 (USD MILLION)
FIGURE 11. ORPHAN DRUGS MARKET SIZE, BY DISTRIBUTION CHANNEL, 2023 VS 2030 (%)
FIGURE 12. ORPHAN DRUGS MARKET SIZE, BY DISTRIBUTION CHANNEL, 2023 VS 2024 VS 2030 (USD MILLION)
FIGURE 13. AMERICAS ORPHAN DRUGS MARKET SIZE, BY COUNTRY, 2023 VS 2030 (%)
FIGURE 14. AMERICAS ORPHAN DRUGS MARKET SIZE, BY COUNTRY, 2023 VS 2024 VS 2030 (USD MILLION)
FIGURE 15. UNITED STATES ORPHAN DRUGS MARKET SIZE, BY STATE, 2023 VS 2030 (%)
FIGURE 16. UNITED STATES ORPHAN DRUGS MARKET SIZE, BY STATE, 2023 VS 2024 VS 2030 (USD MILLION)
FIGURE 17. ASIA-PACIFIC ORPHAN DRUGS MARKET SIZE, BY COUNTRY, 2023 VS 2030 (%)
FIGURE 18. ASIA-PACIFIC ORPHAN DRUGS MARKET SIZE, BY COUNTRY, 2023 VS 2024 VS 2030 (USD MILLION)
FIGURE 19. EUROPE, MIDDLE EAST & AFRICA ORPHAN DRUGS MARKET SIZE, BY COUNTRY, 2023 VS 2030 (%)
FIGURE 20. EUROPE, MIDDLE EAST & AFRICA ORPHAN DRUGS MARKET SIZE, BY COUNTRY, 2023 VS 2024 VS 2030 (USD MILLION)
FIGURE 21. ORPHAN DRUGS MARKET, FPNV POSITIONING MATRIX, 2023
FIGURE 22. ORPHAN DRUGS MARKET SHARE, BY KEY PLAYER, 2023

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